Results 231 to 240 of about 86,084 (265)

Orphan Enzymes?

Science, 2005
Lespinet, Olivier, Labedan, Bernard
openaire   +3 more sources

Orphan Drugs Offer Larger Health Gains but Less Favorable Cost-effectiveness than Non-orphan Drugs

Journal of General Internal Medicine, 2020
James D Chambers, Joshua T Cohen, Peter J Neumann   +2 more
exaly  

The Orphan Patient

New England Journal of Medicine, 1988
W B, Shelley, E D, Shelley
openaire   +2 more sources

Orphan drugs and orphan diseases

European Journal of Paediatric Neurology, 2000
Jaime Campos-Castelló, Gerard Ponsot, François Feillet, M Vidailhet, Irène Maire   +4 more
openaire   +1 more source

Orphans *

2018
openaire   +1 more source

European regulation on orphan medicinal products: 10 years of experience and future perspectives

Nature Reviews Drug Discovery, 2011
Kerstin Westermark, Bruno Sepodes, Brigitte Bloechl-Daum   +2 more
exaly  

Drug repositioning for orphan diseases

Briefings in Bioinformatics, 2011
Anil G Jegga, Cheng Zhu, Minlu Zhang
exaly  

The US Orphan Drug Act: Rare disease research stimulator or commercial opportunity?

Health Policy, 2010
Youwen Zhou
exaly  

Defining orphan conditions in the context of the European orphan regulation: challenges and evolution

Nature Reviews Drug Discovery, 2018
Segundo Mariz, Laura Fregonese, Kristina Larsson   +2 more
exaly  

Orphan Drugs and Their Impact on Pharmaceutical Development

Trends in Pharmacological Sciences, 2018
Misty M Attwood, Mathias Rask-Andersen, Helgi B Schioth   +2 more
exaly