Results 281 to 290 of about 5,265,871 (311)

Orphan drugs and rare diseases: a scientometric review (2000 – 2014)

Expert Opinion on Orphan Drugs, 2014
Chaomei Chen
exaly  

The availability and affordability of orphan drugs for rare diseases in China

Orphanet Journal of Rare Diseases, 2016
Hanjun Sun, Si Jin, Shiwei Gong
exaly  

Rare Diseases, Orphan Drugs, and Orphaned Patients

Molecular Interventions, 2006
openaire   +2 more sources

A Glimmer of Hope for an Orphan Disease

New England Journal of Medicine, 2023
openaire   +2 more sources

Are rare diseases still orphans or happily adopted? The challenges of developing and using orphan medicinal products

British Journal of Clinical Pharmacology, 2006
James Dear, Pajaree Lilitkarntakul
exaly  

The US Orphan Drug Act: Rare disease research stimulator or commercial opportunity?

Health Policy, 2010
Youwen Zhou, Olivier Wellman-Labadie
exaly  

Do payers value rarity? An analysis of the relationship between disease rarity and orphan drug prices in Europe

Journal of Market Access & Health Policy, 2017
Mondher Toumi, Goran Medic, Maarten J. Postma   +2 more
exaly  

Bronchiectasis: Update of an Orphan Disease

American Review of Respiratory Disease, 1988
A F, Barker, E J, Bardana
openaire   +2 more sources

A comparative study of European rare disease and orphan drug markets

Health Policy, 2010
Lut Mergaert, Steven Simoens, Christel Fostier   +2 more
exaly  

„Orphan diseases“

Monatsschrift Kinderheilkunde, 2012
openaire   +1 more source