Results 271 to 280 of about 5,265,871 (311)

Orphan Lung Diseases

Seminars in Respiratory and Critical Care Medicine, 2016
Jay H, Ryu, Luca, Richeldi
openaire   +2 more sources

Bronchiectasis: The disease that was never orphan

Medicina Clínica (English Edition), 2021
openaire   +3 more sources

Orphan diseases and orphan drugs

Comparative Biochemistry and Physiology Part A: Physiology, 1990
openaire   +2 more sources

Orphan drugs and orphan diseases

European Journal of Paediatric Neurology, 2000
Jaime Campos-Castelló, Gerard Ponsot, François Feillet, M Vidailhet, Irène Maire   +4 more
openaire   +1 more source

Analysis of orphan designation status for FDA approved drugs, and case studies in oncology, neuroscience and metabolic diseases

Bioorganic and Medicinal Chemistry, 2023
Dean G Brown
exaly  

Orphan Drug Use in Patients With Rare Diseases: A Population-Based Cohort Study

Frontiers in Pharmacology, 2022
Francesca Gorini, Renzo Guerrini, Paola Parronchi   +2 more
exaly  

The European landscape for gene therapies in orphan diseases: 6-year experience with the EMA Committee for Orphan Medicinal Products

Molecular Therapy, 2023
Segundo Mariz, Kristina Larsson, Eva Malikova   +2 more
exaly  

Policies for Orphan Diseases and Orphan Drugs

2009
x, 115 p.
openaire   +1 more source

Orphan diseases and orphan drugs

Food and Chemical Toxicology, 1987
openaire   +1 more source

Orphan diseases and Orphan drugs

Journal of Pharmaceutical Sciences, 1988
openaire   +1 more source