Results 251 to 260 of about 5,265,871 (311)

Most-Favored-Nation pricing meets Joint Clinical Assessment: early evidence of compounding pressure on European drug launches. [PDF]

J Comp Eff Res
Ramagopalan SV, Ryan ML.
europepmc   +1 more source

Targeting B‐Cell‐Activating Factor and Its Receptor in Immune Thrombocytopenia and Warm Autoimmune Hemolytic Anemia

American Journal of Hematology, Volume 101, Issue 11, Page 2836-2852, November 2026.
ABSTRACT Current treatments for immune thrombocytopenia (ITP) and warm autoimmune hemolytic anemia (wAIHA), rare autoimmune diseases in which autoreactive B cells play a major role, can lead to high response rates; however, for many patients these responses are not durable or maintained after treatment discontinuation.
Matthieu Mahévas, Nichola Cooper, Vickie McDonald, Karina Yazdanbakhsh, Wilma Barcellini   +4 more
wiley   +1 more source

Orphan Designation for Drugs Approved in the United States and European Union: A Comparative Analysis. [PDF]

Clin Pharmacol Ther
Costa E, Ross JS, Kesselheim AS.
europepmc   +1 more source

NOR1 loss relates to inflammation and biological ageing in multiple sclerosis motor cortex. [PDF]

Brain Commun
Unlu Kobya B, Avery A, DeLuca G, Pansieri J.   +3 more
europepmc   +1 more source

Reframing the value of reserve antibiotics: how ultra-orphan reimbursement pathways could offer fair and equitable access to new antibiotics. [PDF]

Health Policy Open
Quinn J, Amersdorffer J, Boysen M, Duffy-Roger O, Hewitt C, Jain M, McKinney D, Ivezic-Schoenfeld Z, Toumi M, Vanbiervliet M, Wasem J.   +10 more
europepmc   +1 more source

Orphan GPCRs in diabetes mellitus: metabolic control, inflammation, and drug development. [PDF]

Front Endocrinol (Lausanne)
Chandrabose S, Muniyandi V, Geddawy A, Thiyagarajan R, Murugesan A, Kandhavelu M.   +5 more
europepmc   +1 more source

Rare disease patients protection: theoretical discussion and institutional construction of orphan drug designation in China. [PDF]

Orphanet J Rare Dis
Zhao X, Zhang M, Zhang M.
europepmc   +1 more source

[Disease of orphans].

Wiadomosci lekarskie (Warsaw, Poland : 1960), 1984
openaire   +1 more source