Results 191 to 200 of about 8,062,145 (231)

Medicine Development and Access for Rare Diseases: Can We Do Better? [PDF]

J Inherit Metab Dis
Hollak CEM, Rosenberg N, Post C, Stolwijk N, Manders E, Schoenmakers D, Penninx B, Reijnhout N, Verdeyen K, Jonker R, Bosch AM, Langeveld M, van der Wel V, de Visser S, van den Berg S.   +14 more
europepmc   +1 more source

Orphan medical devices: addressing the regulatory and access gaps in the EU and US. [PDF]

Front Public Health
Akodad S, Haon B, Rochaix L, Stevens H.
europepmc   +1 more source

Off-label prescribing in pediatrics: between regulatory gaps and clinical evidence. [PDF]

Ital J Pediatr
Marchetti F, Bonati M, Clavenna A.
europepmc   +1 more source

Priced Out of Treatment: The Exorbitant Cost of Antiparasitic Drugs in the United States. [PDF]

Open Forum Infect Dis
Alperin C, Nguyen N, Duffey M, Clark EH.
europepmc   +1 more source

SVEP1 enables efficient binding of angiopoietin-2 to the TIE1 receptor, allowing receptor phosphorylation and downstream signaling. [PDF]

Elife
Uphoff K, Hußmann M, Peters O, Mörgelin M, Metzen F, Obermann WMJ, Bazan FJ, Stetefeld J, Koch M, Schulte-Merker S, Schulte-Ostermann D.   +10 more
europepmc   +1 more source

Methodological challenges in Dutch HTA of non-oncological orphan drugs: a retrospective analysis and price comparison using different pricing models. [PDF]

Orphanet J Rare Dis
Walraven J, Kaveh M, Uyl-de Groot C.
europepmc   +1 more source

Landscape of G Protein-Coupled Receptor Function from Structure Networks. [PDF]

JACS Au
Gentile S, Felline A, Mazzali S, Fanelli F.   +3 more
europepmc   +1 more source

Pulmonary vascular reactivity in severe pulmonary hypertension associated with COPD. [PDF]

ERJ Open Res
Jutant EM, Delarche B, Croquette M, Beurnier A, Diaz A, Bironneau V, Caron F, Riou M, Boucly A, Jaïs X, Savale L, Sitbon O, Bertoletti L, Humbert M, Montani D.   +14 more
europepmc   +1 more source

Regulatory Convergence in Cell and Gene Therapy: Harmonizing Quality, CMC, and Approval Pathways Across the FDA, EMA, PMDA, and Emerging Markets. [PDF]

BioTech (Basel)
Verma N, Arora S.
europepmc   +1 more source