Results 241 to 250 of about 22,884 (253)

The Committee for Orphan Medical Products of the EMEA has adopted a positive opinion recommending orphan drug designation for PI-88

Inpharma Weekly, 2007
openaire   +1 more source

Orphan drug development: the increasing role of clinical pharmacology

Journal of Pharmacokinetics and Pharmacodynamics, 2019
Mariam A Ahmed, Malek Okour, Richard Brundage   +2 more
exaly  

Emergence of orphan drugs in the United States: a quantitative assessment of the first 25 years

Nature Reviews Drug Discovery, 2010
exaly  

Ensuring Effectiveness, Safety, and Access to Orphan Drug Products (1821)

2019
openaire   +1 more source

The Committee for Orphan Medicinal Products of the European Medicines Agency has granted PTC 124 [PTC Therapeutics] orphan drug status

Inpharma Weekly, 2005
openaire   +1 more source

Predictors of orphan drug approval in the European Union

European Journal of Clinical Pharmacology, 2008
exaly  

Flexibility in the FDA approach to orphan drug development

Nature Reviews Drug Discovery, 2017
exaly  

1989 annual survey--133 orphan drug products.

Hospital pharmacy, 1990
openaire   +1 more source

FDA approves ultra-orphan drug on a 4-patient trial

Nature Reviews Drug Discovery, 2015
exaly  

Regulatory policy, value of knowledge assets and innovation strategy: The case of the Orphan Drug Act

Research Policy, 2008
exaly