Results 231 to 240 of about 84,797 (291)

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24‐Month Follow‐Up From the Italian Registry

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane, Giorgia Coratti, Chiara Cutrì, Antonio Varone, Riccardo Masson, Adele D'Amico, Valeria Sansone, Sonia Messina, Federica Ricci, Chiara Ticci, Claudio Bruno, Caterina Agosto, Francesca Benedetti, Antonella Pini, Sabrina Siliquini, Massimiliano Filosto, Alberto Zambon, Ilaria Bitetti, Maria Rosaria Manna, Claudia Dosi, Riccardo Zanin, Stefano Parravicini, Roberto De Sanctis, Giulia Stanca, Michela Catteruccia, Michele Tosi, Irene Mizzoni, Emilio Albamonte, Valentina Franchino, Maria Sframeli, Ilaria Cavallina, Elena Procopio, Michele Sacchini, Simone Morando, Noemi Brolatti, Federica Trucco, Gaia Scarpini, Elena Briganti, Beatrice Berti, Concetta Palermo, Daniela Leone, Stefano C. Previtali, Eugenio Mercuri, the ITASMAC working group   +43 more
wiley   +1 more source

Exploring schoolchildren's perspectives on oral health in a disadvantaged neighbourhood in The Hague - a participatory action research project. [PDF]

BMC Oral Health
Grasveld AE, Bonifácio CC, van der Veen MH.   +2 more
europepmc   +1 more source

Quantifying the Impact of Ocrelizumab on Paramagnetic Rim Lesions in Multiple Sclerosis

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Paramagnetic rim lesions (PRLs) are a subset of chronic active multiple sclerosis (MS) lesions marked by iron‐laden microglia and macrophages. Ocrelizumab, a monoclonal antibody targeting CD20+ B cells, suppresses acute MS activity, but its effect on PRLs remains unclear. In a longitudinal study of 29 ocrelizumab‐treated patients with at least
Kimberly H. Markowitz, Neha V. Safi, Iliana Pliska‐Bloch, Ulrike W. Kaunzner, Ha Luu, Mert Sisman, Yi Wang, Thanh D. Nguyen, Sandra Hurtado Rúa, Susan A. Gauthier   +9 more
wiley   +1 more source

Enhancing undergraduate nursing informatics literacy through design-based learning: a mixed-methods participatory action research study. [PDF]

BMC Nurs
Shen M, Feng Z, Shen Y, Shi Z.
europepmc   +1 more source

Clinical Validation of Plasma p‐217tau in Neurological Diseases

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Plasma p‐217tau is a minimally invasive but specific biomarker for diagnosing Alzheimer's disease (AD). However, its disease specificity remains to be clinically evaluated. We validated the reliability of the p‐217tau biomarker in 12 other neurological diseases.
Takeshi Kawarabayashi, Takumi Nakamura, Ryoma Takahashi, Tetsuya Ueda, Seiji Kinoshita, Chikage Uchida, Takashi Sugawara, Kentaro Hashimoto, Kunihiko Ishizawa, Masakuni Amari, Hiroo Kasahara, Yoshio Ikeda, Masamitsu Takatama, Mikio Shoji   +13 more
wiley   +1 more source

Co-designing roadmaps for promoting culturally relevant food in long-term care homes for the African, Caribbean and Black populations in Canada: a multi-method, participatory action research study protocol. [PDF]

BMC Nutr
Kehoe MacLeod K, Hammond E, Wicks V, Cortbaoui P, Crisp R, Dort J, Dueck C, Fernandez MA, Giroux I, Jessri M, Kamara I, Kapfunde D, Li S, Neufeld H, Onyango E, Otoadese D, Peck S, Reed B, Sinha SK, Muray M.   +19 more
europepmc   +1 more source

Using Participatory Action Research to Enhance Physical Education Interventions for Promoting Active Lifestyles in Schools: A Study Design and Protocol. [PDF]

Healthcare (Basel)
Lizandra J, Valencia-Peris A, Ferriz R, Peiró-Velert C.   +3 more
europepmc   +1 more source

"I never realized how hard recovery is." A quasi-experimental evaluation of a youth participatory action research project for opioid prevention. [PDF]

Am J Community Psychol
Weybright EH, Hampilos K, White AJ, Grinstead C, Fees J, Greer M, Doering EL, Graham LM.   +7 more
europepmc   +1 more source

Enhancing maternity healthcare workers' wellbeing using insider participatory action research. [PDF]

BMC Health Serv Res
Wood CM, Chambers M, Marshall JE.
europepmc   +1 more source