Results 231 to 240 of about 121,342 (296)

Adults With Acid Sphingomyelinase Deficiency Have Sustained Improvements in Clinical Outcomes With up to 5 Years of Olipudase Alfa Enzyme Replacement Therapy: ASCEND Trial Final Results

Journal of Inherited Metabolic Disease, Volume 49, Issue 3, May 2026.
ABSTRACT Acid sphingomyelinase deficiency (ASMD) is a rare debilitating lysosomal storage disease resulting in multisystemic disease manifestations, significant disease burden, and early mortality for some individuals. Enzyme replacement therapy (ERT) with olipudase alfa (Xenpozyme) is the first disease‐specific treatment indicated for noncentral ...
Melissa P. Wasserstein, Carla E. Hollak, Antonio Barbato, Renata C. Gallagher, Roberto Giugliani, Norberto Bernardo Guelbert, Julia B. Hennermann, Takayuki Ikezoe, Robin Lachmann, Olivier Lidove, Paulina Mabe, Eugen Mengel, Maurizio Scarpa, Ebubekir Senates, Michel Tchan, Beth L. Thurberg, Jesus Villarrubia, Nicole M. Armstrong, Shashi Bhushan, Yong Kim, Monica Kumar   +20 more
wiley   +1 more source

Erratum to “Abnormal Exercise Gas Exchange Before Pulmonary Emboli Diagnosis”

Mayo Clinic Proceedings: Innovations, Quality & Outcomes
doaj   +1 more source

Microscopic anatomy of the lungs of domestic animals, mice, and rats. [PDF]

J Vet Diagn Invest
Mulka KR, Gruenwald RC, Yang TS, Caswell JL.   +3 more
europepmc   +1 more source

Dead space in critical care: a practical approach with clinical scenarios. [PDF]

J Anesth Analg Crit Care
Cipulli F, Sanna A, Garberi R, Lassola S, Forcione M, Bellani G, Foti G, Rezoagli E.   +7 more
europepmc   +1 more source

Beyond the PaO₂/FiO₂ ratio: Rethinking ARDS severity through the Lens of physiology. [PDF]

Ann Intensive Care
Al-Husinat L, Khamis R, Azzam S, Trdeh M, Jouryyeh B, Al Sharie S, Touqan M, Alomari A, Nasa P, Schultz MJ, Rocco PR, Battaglini D.   +11 more
europepmc   +1 more source

Enhancing Respiratory Support in COPD Patients with Nasal High Flow Using an Asymmetrical Cannula Interface: A Randomized Cross-Over Study. [PDF]

Int J Chron Obstruct Pulmon Dis
Nilius G, Domanski U, Khalaf M, Schroeder M, Tatkov S.   +4 more
europepmc   +1 more source