Results 31 to 40 of about 236 (216)
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane +43 more
wiley +1 more source
Programas de emprendimiento en instituciones de educación superior
Los emprendimientos universitarios de alto impacto requieren estimular el aprendizaje experiencial y fortalecer lo curricular referente al emprender. Se debe pasar de la teoría a la creación de empresas.
Edward Andrés Benavides-Sánchez +2 more
doaj +1 more source
Cracking the Code: Genotype–Phenotype Correlation Models in Sarcoglycanopathies
ABSTRACT Objective Sarcoglycanopathies are among the most severe limb‐girdle muscular dystrophies (LGMD), though milder presentations have been described. These diseases are primarily caused by missense variants, but the limited predictability of their effect on protein maturation, complex formation, and transport has hindered reliable genotype ...
Leonela Luce +72 more
wiley +1 more source
Objective JAK inhibitors (JAKis) have shown promising effects in early‐phase studies of SSc. We aimed to assess the safety and explore effectiveness of JAKis compared to conventional immunosuppressants in SSc. Methods A longitudinal retrospective study of the EUSTAR cohort was performed.
Stefano Di Donato +27 more
wiley +1 more source
El ranking Times en el mercado del prestigio universitario
El presente artículo analiza el World University Ranking del Times Higher Education (THE), una de las clasificaciones internacionales de universidades más conocidas e influyentes. Se pone especial atención en el diseño y construcción metodológica del ranking.
Imanol Ordorika +1 more
openaire +2 more sources
Rankings universitarios, ni ángeles ni demonios: críticas y usos por parte de grupos de interés
El entorno de las universidades ha experimentado un cambio significativo en los últimos años, debido a una mayor competencia por recursos y la presión por demostrar que están cumpliendo con sus misiones y objetivos de manera efectiva. Esto ha generado la necesidad de evaluar su quehacer y exhibir su desempeño, espacio que han ocupado los rankings de ...
Francisco Ganga-Contreras +3 more
openaire +1 more source
AI‐Assisted Workflow for (Scanning) Transmission Electron Microscopy: From Data Analysis Automation to Materials Knowledge Unveiling. Abstract (Scanning) transmission electron microscopy ((S)TEM) has significantly advanced materials science but faces challenges in correlating precise atomic structure information with the functional properties of ...
Marc Botifoll +19 more
wiley +1 more source
Our meta‐analysis showed significant improvement of PFS with lenalidomide, proteasome inhibitors, and CD38‐based therapies. A significant OS benefit was noted only with lenalidomide in transplant‐eligible (TE) patients, while CD38‐directed therapy showed a trend toward improved OS.
Heinz Ludwig +25 more
wiley +1 more source
Dentro de los instrumentos de evaluación más destacados en el contexto internacional, se encuentran los rankings universitarios Academic Ranking World Universities (ARWU), el Times Higher Education (THE), y el Quacquarelli Symond (QS).
Patricia Moctezuma Hernández +3 more
doaj
Rankings na educação superior: as melhores faculdades do Brasil (1982-2000)
Este artigo aborda o estudo do extinto ranking Melhores Faculdades, o primeiro no campo da educação superior brasileira, criado em 1981 e editado anualmente, por dezenove anos, pela revista masculina Playboy.
Adolfo Ignacio Calderón +2 more
doaj +1 more source

