Results 31 to 40 of about 236 (216)

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24‐Month Follow‐Up From the Italian Registry

open access: yesAnnals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane   +43 more
wiley   +1 more source

Programas de emprendimiento en instituciones de educación superior

open access: yesRevista Escuela de Administracion de Negocios, 2022
Los emprendimientos universitarios de alto impacto requieren estimular el aprendizaje experiencial y fortalecer lo curricular referente al emprender. Se debe pasar de la teoría a la creación de empresas.
Edward Andrés Benavides-Sánchez   +2 more
doaj   +1 more source

Cracking the Code: Genotype–Phenotype Correlation Models in Sarcoglycanopathies

open access: yesAnnals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Sarcoglycanopathies are among the most severe limb‐girdle muscular dystrophies (LGMD), though milder presentations have been described. These diseases are primarily caused by missense variants, but the limited predictability of their effect on protein maturation, complex formation, and transport has hindered reliable genotype ...
Leonela Luce   +72 more
wiley   +1 more source

Real‐World Safety and Effectiveness of JAK Inhibitors in Systemic Sclerosis: A Propensity‐Matched Study from the EUSTAR Cohort

open access: yesArthritis Care &Research, Accepted Article.
Objective JAK inhibitors (JAKis) have shown promising effects in early‐phase studies of SSc. We aimed to assess the safety and explore effectiveness of JAKis compared to conventional immunosuppressants in SSc. Methods A longitudinal retrospective study of the EUSTAR cohort was performed.
Stefano Di Donato   +27 more
wiley   +1 more source

El ranking Times en el mercado del prestigio universitario

open access: yesPerfiles Educativos, 1969
El presente artículo analiza el World University Ranking del Times Higher Education (THE), una de las clasificaciones internacionales de universidades más conocidas e influyentes. Se pone especial atención en el diseño y construcción metodológica del ranking.
Imanol Ordorika   +1 more
openaire   +2 more sources

Rankings universitarios, ni ángeles ni demonios: críticas y usos por parte de grupos de interés

open access: yesJournal of the Academy, 2023
El entorno de las universidades ha experimentado un cambio significativo en los últimos años, debido a una mayor competencia por recursos y la presión por demostrar que están cumpliendo con sus misiones y objetivos de manera efectiva. Esto ha generado la necesidad de evaluar su quehacer y exhibir su desempeño, espacio que han ocupado los rankings de ...
Francisco Ganga-Contreras   +3 more
openaire   +1 more source

Artificial Intelligence‐Assisted Workflow for Transmission Electron Microscopy: From Data Analysis Automation to Materials Knowledge Unveiling

open access: yesAdvanced Materials, EarlyView.
AI‐Assisted Workflow for (Scanning) Transmission Electron Microscopy: From Data Analysis Automation to Materials Knowledge Unveiling. Abstract (Scanning) transmission electron microscopy ((S)TEM) has significantly advanced materials science but faces challenges in correlating precise atomic structure information with the functional properties of ...
Marc Botifoll   +19 more
wiley   +1 more source

The Changing Landscape of Maintenance Therapy in Newly Diagnosed Multiple Myeloma: A Systematic Review With Network Meta‐Analysis of the European Myeloma Network (EMN)

open access: yesAmerican Journal of Hematology, EarlyView.
Our meta‐analysis showed significant improvement of PFS with lenalidomide, proteasome inhibitors, and CD38‐based therapies. A significant OS benefit was noted only with lenalidomide in transplant‐eligible (TE) patients, while CD38‐directed therapy showed a trend toward improved OS.
Heinz Ludwig   +25 more
wiley   +1 more source

Evaluación de la calidad de la educación superior en México: comparación de los indicadores de rankings universitarios nacionales e internacionales

open access: yesRIESED, 2015
Dentro de los instrumentos de evaluación más destacados en el contexto internacional, se encuentran los rankings universitarios Academic Ranking World Universities (ARWU), el Times Higher Education (THE), y el Quacquarelli Symond (QS).
Patricia Moctezuma Hernández   +3 more
doaj  

Rankings na educação superior: as melhores faculdades do Brasil (1982-2000)

open access: yesEstudos em Avaliação Educacional, 2014
Este artigo aborda o estudo do extinto ranking Melhores Faculdades, o primeiro no campo da educação superior brasileira, criado em 1981 e editado anualmente, por dezenove anos, pela revista masculina Playboy.
Adolfo Ignacio Calderón   +2 more
doaj   +1 more source

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