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Tezacaftor for the treatment of cystic fibrosis
Expert Review of Respiratory Medicine, 2018Cystic fibrosis (CF) is the most common, life-limiting autosomal recessive disease in Caucasians, and is caused by defects in production of the CFTR ion channel. Until recently, there were no available treatments targeting the disease-causing defects in CFTR but newly developed CFTR modulators are changing the course of disease in CF.
Marc A Sala, Manu Jain
exaly +3 more sources
Elexacaftor/ivacaftor/tezacaftor/ivacaftor/tezacaftor
Reactions Weekly, 2021openaire +1 more source