Results 151 to 160 of about 6,598 (226)

664 Effectiveness and safety of elexacaftor/tezacaftor/ivacaftor therapy: An Italian center experience

, 2022
E. Nazzari, G. Bischetti, C. Sciarrabba, A. Mariani, G. Alicandro, A. Biffi, C. Colombo   +6 more
openalex   +1 more source

Lung transplant referral for individuals with cystic fibrosis: Cystic Fibrosis Foundation consensus guidelines [PDF]

, 2019
CF Lung Transplant Referral Guidelines Committee,, Dunitz, Jordan M, Faro, Albert, Gray, Alice L, Hempstead, Sarah E, Lucy, Amy, McKone, Edward F, Pilewski, Joseph M, Ramos, Kathleen J, Rosenbluth, Daniel B, Smith, Patrick J, Tallarico, Erin   +11 more
core   +1 more source

L467F;F508del Complex Allele in a Heterozygous State with CFTRdele2,3: What to Expect from CFTR Modulators? [PDF]

Int J Mol Sci
Kondratyeva E, Efremova A, Melyanovskaya Y, Krasnova M, Milovanov M, Shchagina O, Stepanova A, Voronkova A, Sherman V, Kutsev S, Goldshtein D.   +10 more
europepmc   +1 more source

Impact of Elexacaftor-Tezacaftor-Ivacaftor on Gastrointestinal Symptoms, Intestinal Ultrasound, and Pancreatic Stiffness in Cystic Fibrosis. [PDF]

Clin Transl Gastroenterol
Fraquelli M, Piagnani A, Corti F, Lanfranchi C, Casazza G, Colombo C.   +5 more
europepmc   +1 more source

131 In vitro responses of F508DEL human nasal epithelial cells correlate with clinical improvement with elexacaftor-tezacaftor-ivacaftor

, 2023
Moemen S. Hanafy, C. Fernandez-Petty, R. Joseph, K. Vijaykumar, G. Tearney, Steven M. Rowe, G. Solomon   +6 more
openalex   +1 more source

Assessment of efficacy and tolerability of elexacaftor-tezacaftor-ivacaftor in an observational cohort study of "aged" people with cystic fibrosis. [PDF]

Ther Adv Respir Dis
Blankenship S, Flueckiger BV, Caleb G, Bailey J, Baker E, Garcia B, Krick S.   +6 more
europepmc   +1 more source

Cystic Fibrosis and CFTR Modulators: The Impact on Bone Density, Muscle Mass and Strength in Children and Young Adolescents. [PDF]

Children (Basel)
Iordanidou K, Karakousis ND, Hatziagorou E, Chrysochoou EA, Galogavrou M, Sopiadou A, Papagianni M.   +6 more
europepmc   +1 more source

Successful Pregnancy in a Cystic Fibrosis Patient with a Severe Impairment of Lung Function Receiving Elexacaftor-Tezacaftor-Ivacaftor

, 2022
Zisis Balmpouzis, Annabelle Faure van Rossum, David Baud, Alice Panchaud, Georgia Mitropoulou, Jesica Mazza Stalder, Angela Koutsokera   +6 more
openalex   +1 more source

CFTR rescue in W1282X cystic fibrosis patient-derived intestinal organoids (PDIOs) mediated by translational readthrough-inducing drugs (TRIDs). [PDF]

Genet Med Open
Perriera R, Ramalho AS, Vermeulen F, Vitale E, Pibiri I, Pace A, Lentini L.   +6 more
europepmc   +1 more source

Impact of Cystic Fibrosis Transmembrane Conductance Regulator Modulating Therapies on Liver Transplant Outcomes. [PDF]

Gastro Hep Adv
Naimimohasses S, Ray A, Tan E, Wiggins A, Hasjim BJ, Chen S, Bhat M.   +6 more
europepmc   +1 more source