Results 161 to 170 of about 6,598 (226)
Severe hepatotoxicity is uncommon following the introduction of Elexacaftor/Tezacaftor/Ivacaftor: A real-world two-years follow-up study of the Danish cystic fibrosis cohort [PDF]
Christine Højte, Mette Frahm Olsen, Daniel Faurholt‐Jepsen, Marianne Hørby Jørgensen, Tacjana Pressler, Christian Leo‐Hansen, Thomas Bryrup, Majbritt Jeppesen, Hanne Vebert Olesen, Janne Petersen, Terese L. Katzenstein, Bibi Uhre Nielsen, Marianne Nielsine Skov +12 moreopenalex +1 more sourceBody mass, linear growth, and body composition before and after the introduction of elexacaftor/tezacaftor/ivacaftor among children and adults with cystic fibrosis
Karlen S Bader-Larsen, Bibi Uhre Nielsen, E. Henriksen, Thomas Bryrup, Christian Leo‐Hansen, Inger Hee Mabuza Mathiesen, Daniel Faurholt‐Jepsen, Tavs Qvist, Peter Oturai, Bente Langdahl, Majbritt Jeppesen, Hanne Olsen, Tacjana Pressler, Marianne Nielsine Skov, Mette Frahm Olsen, Esben Herborg Henriksen, Christine Højte, Majbritt Jeppesen, Søren Jensen‐Fangel, Camilla Bjørn Jensen, Terese Katzentein, Karlen S Bader-Larsen, Christian Leo‐Hansen, Hanne Vebert Olesen, Mette Frahm Olsen, Janne Petersen, Tacjana Pressler, Tavs Qvist, Hans Kristian Pedersen, Espen Jimenez‐Solem, Joanna Wang, Tavs Qvist, Hans Kristian Råket, Marianne Skov, Espen Jimenez Solem, Joanna Nan Wang +35 moreopenalex +1 more sourceThe expanded French compassionate programme for elexacaftor–tezacaftor–ivacaftor use in people with cystic fibrosis without a F508del CFTR variant: a real-world study
Pierre‐Régis Burgel, Isabelle Sermet‐Gaudelus, Emmanuelle Girodon, I. Durieu, Véronique Houdouin, Camille Audousset, Julie Macey, Dominique Grenet, Michele Porzio, M. Murris‐Espin, Philippe Reix, Mélisande Baravalle, Chantal Belleguic, Laurent Mély, Juliette Verhille, Laurence Weiss, Martine Reynaud‐Gaubert, Marie Mittaine, Rébecca Hamidfar, Sophie Ramel, Laure Cosson, Benoît Douvry, Isabelle Danner‐Boucher, P. Foucaud, Charlotte Roy, Espérie Burnet, Caroline Raynal, M.‐P. Audrézet, Jennifer Da Silva, Clémence Martin, Reem Kanaan, Nicolas Carlier, Isabelle Honoré, F. Chedevergne, Elise Dréano, Aurélie Hatton, Alexandre Hinzpeter, Iwona Pranke, Laurence Le Clainche-Viala, Sophie Mayer, Harriet Corvol, Guillaume Thouvenin, Sandra de Miranda, Natascha Remus, Benoît Douvry, L. Duthoit, T. Pérez, Olivier Le Rouzic, Nathalie Wizla, Claire Bon, S. Bui, Nora Poey, Nathalie Stremler, Bérengère Coltey, Nadine Dufeu, Jean Lebihan, Asma Gabsi, Delphine Pouradier, Claire Andréjak, Cinthia Rames, Magali Dupuy-Grasset, Jeanne Languepin, Christophe Marguet, S. Pramil, Baptiste Arnouat, Annlyse Fanton, Michel Abély, Bruno Ravoninjatovo, Aurore Blondé, Anne Guillaumot, Sébastien Kieffer, Aurélie Tatopoulos, R. Nové-Josserand, Camille Ohlmann, Thomas Perrin, Quitterie Reynaud, C. Llerena, S. Quétant, Sophie Valois, Marie‐Laure Dalphin, Bénédicte Richaud-Thiriez, Eric Deneuville, R. Chiron, Floriane Socchi, Tiphaine Bihouée, Julie Mankikian, Thomas Flament, Nathalie Coolen-Allou, Elsa Gachelin, Caroline Périsson, Constance Vuillard, Marion Dupuis, Wael Alkoussa, Sarah Marchal, Sylvie Leroy, Manuëla Scalbert, Karine Campbell, Muriel Laurans, Guillaume Labbé, Sylvie Montcouquiol +99 moreopenalex +2 more sources