Results 41 to 50 of about 8,926 (205)

A phase 1/2 safety and efficacy study of TAK‐754 gene therapy: The challenge of achieving durable factor VIII expression in haemophilia A clinical trials

open access: yesHaemophilia, Volume 31, Issue 1, Page 108-117, January 2025.
Abstract Introduction Haemophilia A is an X‐linked bleeding disorder resulting from a deficiency of factor VIII (FVIII). To date, multiple gene therapies have entered clinical trials with the goal of providing durable haemostatic protection from a single dose. TAK 754 (BAX 888) is an investigational AAV8‐based gene therapy containing a FVIII transgene.
John Chapin   +13 more
wiley   +1 more source

Trombosis de válvulas cardiacas biológicas. Presentación de dos casos evaluados con ecocardiografía 3D en tiempo real

open access: yesRevista Colombiana de Cardiología, 2011
La trombosis de las válvulas protésicas biológicas es una complicación infrecuente, que se asocia con mortalidad elevada. En este artículo se reporta el caso de un paciente de género masculino, de 72 años de edad, con prótesis valvular biológica en ...
Jairo A. Rendón, MD   +1 more
doaj   +1 more source

SÍNDROME DE PLAQUETAS PEGAJOSAS: REPORTE DE CASO

open access: yesRevista Médica de la Universidad de Costa Rica, 2022
El Síndrome de Plaquetas Pegajosas es un trastorno autosómico dominante caracterizado por alteraciones de la agregación plaquetaria en respuesta a la epinefrina y/o el fosfato de adenosina, el cual favorece fenómenos trombóticos arteriales y venosos ...
Daniel Casares-Fallas   +1 more
doaj   +1 more source

Humanistic burden of haemophilia A without inhibitors: A cross‐sectional analysis of the HemoLIFE study

open access: yesHaemophilia, Volume 30, Issue 4, Page 950-958, July 2024.
Abstract Aim To evaluate the impact of haemophilia A without inhibitors on humanistic outcomes in patients and caregivers. Herein, we report a cross‐sectional analysis of the baseline data of persons with haemophilia (PWH) participating in the prospective study HEMOLIFE. Methods These data are part of a prospective, observational, and multicentre study
María Teresa Álvarez‐Román   +11 more
wiley   +1 more source

Trombosis venosa profunda

open access: yesRECIMUNDO, 2019
Este trabajo sintetiza el conocimiento de la enfermedad conocida como trombosis venosa profunda (TVP), a través de una revisión bibliográfica acerca de esta patología que proporciona información importante para el desarrollo del trabajo de investigación. Mediante el proceso de investigación se observa, que la trombosis venosa profunda es una enfermedad
Lisbeth Xiomara Valverde Barragán   +3 more
openaire   +1 more source

Trombosi venose cerebrali

open access: yesEMC - AKOS - Trattato di Medicina, 2010
Le trombosi venose cerebrali rappresentano una rara varieta di accidente vascolare cerebrale che puo colpire persone di ogni eta. Tenuto conto della diversita delle loro eziologie, esse possono essere riscontrate in tutte le discipline. Hanno anche una presentazione clinica molto varia, che rende la loro diagnosi spesso difficile.
J. Mawet, I. Crassard, M.-G. Bousser
openaire   +1 more source

Complement and transplant‐associated thrombotic microangiopathy: Current and future approaches

open access: yes
HemaSphere, Volume 10, Issue 4, April 2026.
Massimo Cugno   +2 more
wiley   +1 more source

The role of the specialist nurse in comprehensive care for bleeding disorders in Europe: An integrative review

open access: yesHaemophilia, Volume 30, Issue 3, Page 598-608, May 2024.
Abstract Introduction Managing bleeding disorders (BDs) is complex, requiring a comprehensive approach coordinated by a multidisciplinary team (MDT). Haemophilia nurses (HNs) play a central role in the MDT, frequently coordinating care. As novel treatments bring change to the treatment landscape, ongoing education and development is key.
Greta Mulders   +7 more
wiley   +1 more source

The psychosocial impact of haemophilia from patients’ and caregivers’ point of view: The results of an Italian survey

open access: yesHaemophilia, Volume 30, Issue 2, Page 449-462, March 2024.
Abstract Backgroud A huge amount of data about psychosocial issues of people with haemophilia (PwH) are available; however, these materials are fragmentary and largely outdated, failing to reflect the impact of current treatment strategies. Aim Describing the influence of illness on psychosocial aspects of adult PwH (≥18 years) and caregivers of ...
Arianna Fornari   +15 more
wiley   +1 more source

Trombosis venosa cerebral [PDF]

open access: yesActa Médica Grupo Ángeles, 2021
Itzel Ariadna Hernández Dehesa   +2 more
openaire   +1 more source

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