Results 161 to 170 of about 872,130 (197)

Achieving clinically meaningful changes in haemoglobin levels in patients with non-transfusion-dependent β-thalassaemia treated with luspatercept: A post hoc analysis of the phase 2 BEYOND trial. [PDF]

Br J Haematol
Musallam KM, Taher AT, Porter JB, Kattamis A, Glassberg MB, Bueno LM, Martin-Regueira P, Reverte M, Medlin LF, Dyer M, Wang K, Cappellini MD.   +11 more
europepmc   +1 more source

Routine management, healthcare resource use and patient and carer-reported outcomes of patients with transfusion-dependent β-thalassaemia in the United Kingdom: A mixed methods observational study. [PDF]

EJHaem, 2021
Shah F, Telfer P, Velangi M, Pancham S, Wynn R, Pollard S, Chalmers E, Kell J, Carter AM, Hickey J, Paramore C, Jobanputra M, Ryan K.   +12 more
europepmc   +1 more source

The wide spectrum of β-thalassaemia intermedia-induced pulmonary hypertension: two case reports on the possible role of specific pulmonary arterial hypertension therapy. [PDF]

Pulm Circ, 2021
Anthi A, Tsiapras D, Karyofyllis P, Voudris V, Armaganidis A, Orfanos SE.   +5 more
europepmc   +1 more source

The structure and expression of mammalian gene clusters [PDF]

, 1982
Grosveld, F., Flavell, R.A. (Richard), Flavell, Richard A., Moschonas, N., Weiss, E.H. (Elisabeth), Kleine, A. de, Boer, E. de, Klein, J.E.M.M. (Annelies) de, Golden, L., Mellor, Andrew L., Boer, E. (Ernie) de, Bullman, H., Busslinger, M., Groffen, J., Bud, H., Weiss, Elisabeth H., Mellor, A.L., Grosveld, F.G. (Frank)   +17 more
core   +1 more source

A review of genetic modification for ex vivo cellular therapies

Transfusion, Volume 66, Issue S2, Page S45-S57, September 2026.
Anh Dinh, Nan Zhang, David Stroncek
wiley   +1 more source

Long-term efficacy and safety of mitapivat in non-transfusion-dependent α- or β-thalassaemia: An open-label phase 2 study. [PDF]

Br J Haematol
Kuo KHM, Layton DM, Lal A, Vichinsky EP, Dahlin JL, Shen S, Price GM, Gilroy KS, Estepp JH, Al-Samkari H.   +9 more
europepmc   +1 more source

Impaired physical ability in patients with transfusion-dependent β-thalassaemia: Can regular physical activity be a countermeasure? [PDF]

Br J Haematol
Noguer M, Berthon P, Makowski C, Messonnier LA.   +3 more
europepmc   +1 more source

Non-Invasive Determination of the Paternal Inheritance in Pregnancies at Risk for β-Thalassaemia by Analyzing Cell-Free Fetal DNA Using Targeted Next-Generation Sequencing. [PDF]

Int J Mol Sci
Byrou S, Brouwer RWW, Tomazou M, Tamana S, Kountouris P, Lederer CW, Petrou M, Ozgur Z, den Dekker X, Azmani Z, Christou S, Makariou C, Kleanthous M, IJcken WFJV, Papasavva T.   +14 more
europepmc   +1 more source

Health-related quality of life and associated factors among children with Transfusion-dependent β-thalassaemia: a cross-sectional study in Guangxi Province. [PDF]

Health Qual Life Outcomes
Qiao J, Luo B, Ming J, Zhang X, Weng J, Deng Q, Zhou S, Chen Y.   +7 more
europepmc   +1 more source

Deferoxamine, deferasirox, and deferiprone triple iron chelator combination therapy for transfusion-dependent β-thalassaemia with very high iron overload: a randomised clinical trial. [PDF]

Lancet Reg Health Southeast Asia
Premawardhena A, Wanasinghe S, Perera C, Wijethilaka MN, Rajakaruna RHMG, Samarasinghe RANKK, Williams S, Mettananda S.   +7 more
europepmc   +1 more source