Results 81 to 90 of about 72,368 (157)

Programmable Single-Stranded Circular Antisense Oligonucleotides for Multitarget Gene Therapy. [PDF]

JACS Au
Pan Y, Li X, Zhu C, Wang M, Wu Y, Xu R, Wu J, Chen R, Jiang Y, Tian B, Dong Y, Liu D.   +11 more
europepmc   +1 more source

Behavioral improvement in dystrophic <i>mdx23</i> mouse following repeated antisense oligonucleotides injections. [PDF]

Mol Ther Nucleic Acids
Aghaeipour A, Mitsogiannis M, Fergus C, Tetorou K, Gileadi T, Stojek E, Talavera S, Singh S, Siddle M, Prendeville J, Sokolowska E, Kelly V, Morgan J, Montanaro F, Muntoni F.   +14 more
europepmc   +1 more source

Tofersen and other antisense oligonucleotides in ALS. [PDF]

Ther Adv Neurol Disord
Ludolph A, Wiesenfarth M.
europepmc   +1 more source

Expansion of Splice-Switching Therapy with Antisense Oligonucleotides. [PDF]

Int J Mol Sci
Takeshima Y.
europepmc   +1 more source

SNA-modified antisense oligonucleotides: A new pathway for renal targeting? [PDF]

Mol Ther Nucleic Acids
Dumoulin B, Yamada K, Susztak K.
europepmc   +1 more source

Acute neuronal inhibition response caused by phosphorothioate antisense oligonucleotides following local delivery to the central nervous system. [PDF]

Nucleic Acids Res
O'Rourke JG, Bachmann G, Mazur C, Zhou K, Platoshyn O, Bravo Hernandez M, Klein SK, Nguyen J, Burel S, Hoffmaster C, Zanardi T, Jafar-Nejad P, Marsala M, Henry SP, Swayze EE, Powers B, Kordasiewicz HB.   +16 more
europepmc   +1 more source

Structural Characterization of <i>DDX23</i> 5' UTR Regulatory Elements and Their Targeting by LNA-Modified Antisense Oligonucleotides. [PDF]

Int J Mol Sci
Kamzeeva P, Shepelev N, Zabbarova V, Brylev V, Chistov A, Ryazantsev D, Kot E, Novopashina D, Rubtsova M, Aralov A.   +9 more
europepmc   +1 more source

Single Antisense Oligonucleotides Correct Diverse Splicing Mutations in Hotspot Exons. [PDF]

Proc Natl Acad Sci U S A
Duan C, Rong S, Buerer L, Neil CR, Zhong Y, Lyu Z, Savatt JM, Strande NT, Fairbrother WG.   +8 more
europepmc   +1 more source