Longitudinal data collection in pediatric and adult patients with 5q spinal muscular atrophy in Latin America: LATAM RegistrAME study - a clinical registry study protocol. [PDF]
Batista EC +7 more
europepmc +1 more source
[Multifocal motor neuropathy. Report of three cases at a reference hospital in Mexico]. [PDF]
Aguilar-Vázquez CA +4 more
europepmc +1 more source
[Juvenile Pompe disease: Undescribed genotype. First report in Quintana Roo]. [PDF]
Flores-Gonzale A +5 more
europepmc +1 more source
A Rare Guillain-Barré Syndrome Variant with Multi-Ganglioside Reactivity: A Case of Severe Cranial Nerve Involvement. [PDF]
Gómez-Dabó L +11 more
europepmc +1 more source
Quality of life assessment instruments in children and adolescents with neuromuscular diseases: a systematic scoping review. [PDF]
Cruz KLT +3 more
europepmc +1 more source
A state-of-the-art review of registries in spinal muscular atrophy: A valuable resource for clinical research. [PDF]
Balaji L +3 more
europepmc +1 more source
[Comunicaciones LXI Reunión Anual de la SENFC Granada, 29 a 31 de Octubre de 2025]. [PDF]
europepmc +1 more source
AMEsobreRuedas Early Powered Mobility in Children with Spinal Muscular Atrophy Type I: Protocol of a Randomized Controlled Trial. [PDF]
Palomo-Carrión R +9 more
europepmc +1 more source
Judicialization of Zolgensma in the Ministry of Health: costs and clinical profile of patients. [PDF]
Kretzschmar AKM +3 more
europepmc +1 more source

