ACO-SWITCH: Rationale and Design of a Phase 4 Study Evaluating Serum Transthyretin in ATTR-CM After Switching from Tafamidis to Acoramidis. [PDF]
Pfister R +6 more
europepmc +1 more source
Visual scoring of bone scintigraphy in ATTR-CM: insights from the TTRACK study. [PDF]
Tingen HSA, Gorter TM, Slart RHJA.
europepmc +1 more source
CRISPR-Cas9 Gene Editing with Nexiguran Ziclumeran for ATTR Cardiomyopathy [PDF]
BACKGROUND: Transthyretin amyloidosis with cardiomyopathy (ATTR-CM) is a progressive, often fatal disease. Nexiguran ziclumeran (nex-z) is an investigational therapy based on CRISPR-Cas9 (clustered regularly interspaced short palindromic repeats and ...
Walsh, Liron +19 more
core
Plain language summary of how acoramidis affects the total number of heart problems over time in people with ATTR-CM: findings from the ATTRibute-CM study. [PDF]
Masri A +21 more
europepmc +1 more source
reservedIntroduzione: L’amiloidosi da transtiretina wild type (ATTR-wt) è una patologia sistemica progressiva acquisita, che interessa prevalentemente i soggetti anziani di sesso maschile. La manifestazione primaria della patologia è lo sviluppo di una
RAMPOGNA, MATILDE
core
Efficacy of tafamidis across age groups in ATTR-CM: insights from real-world data. [PDF]
Gregório C +10 more
europepmc +1 more source
<i>In-vivo</i> CRISPR editing for ATTR-CM: therapeutic transthyretin silencing through hepatic genome correction. [PDF]
Tahir A +4 more
europepmc +1 more source
Real-World Efficacy of Tafamidis in Korean ATTR-CM Patients: A Retrospective Observational Strain Analysis. [PDF]
Shin H +9 more
europepmc +1 more source
Functionally Limiting Symptoms and Inability to Independently Complete Daily Activities Increase the Burden Felt by Caregivers to Patients with ATTR-CM. [PDF]
Cappelli F +9 more
europepmc +1 more source
Tc-99 m Pyrophosphate Uptake in Atrial Amyloidosis With Hemorrhagic Mass - A Diagnostic Pitfall Mimicking ATTR-CM. [PDF]
Fujimoto N +3 more
europepmc +1 more source

