Results 111 to 120 of about 5,299 (208)

Impact of CFTR modulator concentrations on clinical response in cystic fibrosis. [PDF]

Eur Respir J
Chalamalla AR, Baker E, Ryan KJ, Dowell A, Natt JR, Zemanick ET, Konstan MW, Mayer-Hamblett N, Acosta EP, Guimbellot JS, CHEC-SC investigators.   +10 more
europepmc   +1 more source

Predictive capacity of paediatric nasal epithelial cells in sequential CFTR modulator therapy. [PDF]

Thorax
Fawcett LK, Chew ZA, Schneider-Futschik EK, Allan KM, Patel HR, Jaffe A, Waters S.   +6 more
europepmc   +1 more source

Psychological impact of genetic eligibility for CFTR modulator therapy in children with cystic fibrosis and their parents. [PDF]

Eur J Pediatr
Oztosun B, Durcan G, Gulumser SB, Altug D, Gunal B, Anac E, Yavuz M, Cokugras H, Dogangun B, Kilinc Sakalli AA.   +9 more
europepmc   +1 more source

AI-driven breathomics for early detection of CFTR modulator resistance in cystic fibrosis. [PDF]

Ann Med Surg (Lond)
Khan MH, Tariq AU, Cheema WA, Fatima M.
europepmc   +1 more source

Optimizing CFTR modulator therapy management for cystic fibrosis through the ReX platform. [PDF]

Front Pediatr, 2023
Yaacoby-Bianu K, Cohen-Cymberknoh M, Shoseyov D, Lavi T, Ostrovski A, Shteinberg M, Livnat G.   +6 more
europepmc   +1 more source

Advances in cystic fibrosis: CFTR modulator triple combinations. [PDF]

Eur Respir J
Burgel PR, Mall MA.
europepmc   +1 more source

Understanding and addressing the needs of people with cystic fibrosis in the era of CFTR modulator therapy. [PDF]

Lancet Respir Med, 2023
Hisert KB, Birket SE, Clancy JP, Downey DG, Engelhardt JF, Fajac I, Gray RD, Lachowicz-Scroggins ME, Mayer-Hamblett N, Thibodeau P, Tuggle KL, Wainwright CE, De Boeck K.   +12 more
europepmc   +1 more source

RFFL antisense oligonucleotides: A novel stabilization strategy to broaden the reach of CFTR modulator therapy. [PDF]

Mol Ther Nucleic Acids
Pedemonte N.
europepmc   +1 more source

Impact of Highly Effective CFTR Modulator Therapy on Physical Activity, Sleep, and Sinonasal Symptoms in Preschool Children with Cystic Fibrosis: A Prospective Single-Center Pilot Study. [PDF]

Adv Respir Med
Schellhorn S, Schmidt H, Janda A, Gülke D, Toth M, Fabricius D, Bode SFN.   +6 more
europepmc   +1 more source

Personalized CFTR Modulator Therapy for G85E and N1303K Homozygous Patients with Cystic Fibrosis. [PDF]

Int J Mol Sci, 2023
Graeber SY, Balázs A, Ziegahn N, Rubil T, Vitzthum C, Piehler L, Drescher M, Seidel K, Rohrbach A, Röhmel J, Thee S, Duerr J, Mall MA, Stahl M.   +13 more
europepmc   +1 more source