Results 181 to 190 of about 1,459,532 (261)

Psychological impact of genetic eligibility for CFTR modulator therapy in children with cystic fibrosis and their parents. [PDF]

Eur J Pediatr
Oztosun B, Durcan G, Gulumser SB, Altug D, Gunal B, Anac E, Yavuz M, Cokugras H, Dogangun B, Kilinc Sakalli AA.   +9 more
europepmc   +1 more source

AI-driven breathomics for early detection of CFTR modulator resistance in cystic fibrosis. [PDF]

Ann Med Surg (Lond)
Khan MH, Tariq AU, Cheema WA, Fatima M.
europepmc   +1 more source

Optimizing CFTR modulator therapy management for cystic fibrosis through the ReX platform. [PDF]

Front Pediatr, 2023
Yaacoby-Bianu K, Cohen-Cymberknoh M, Shoseyov D, Lavi T, Ostrovski A, Shteinberg M, Livnat G.   +6 more
europepmc   +1 more source

Advances in cystic fibrosis: CFTR modulator triple combinations. [PDF]

Eur Respir J
Burgel PR, Mall MA.
europepmc   +1 more source

RFFL antisense oligonucleotides: A novel stabilization strategy to broaden the reach of CFTR modulator therapy. [PDF]

Mol Ther Nucleic Acids
Pedemonte N.
europepmc   +1 more source

Impact of Highly Effective CFTR Modulator Therapy on Physical Activity, Sleep, and Sinonasal Symptoms in Preschool Children with Cystic Fibrosis: A Prospective Single-Center Pilot Study. [PDF]

Adv Respir Med
Schellhorn S, Schmidt H, Janda A, Gülke D, Toth M, Fabricius D, Bode SFN.   +6 more
europepmc   +1 more source

Transcriptomic and functional responses of the cystic fibrosis airway epithelium to CFTR modulator therapy. [PDF]

JCI Insight
Vladar EK, Gillen AE, Yadav S, Murphree MR, Baraghoshi D, Harris JK, Pruesse E, Niemiec SS, Wilson AW, Hisert KB, Humphries SM, Strand M, Lynch DA, Seibold MA, Beswick DM, Taylor-Cousar JL.   +15 more
europepmc   +1 more source

Functional, Cohort-Level Assessment of CFTR Modulator Responses Using Biobanked Nasal Epithelial Cells from Individuals with Cystic Fibrosis. [PDF]

J Pers Med
Aalbers BL, Amatngalim GD, Aarts EM, Rodenburg LW, den Hertog-Oosterhoff LA, Heijerman HGM, Beekman JM.   +6 more
europepmc   +1 more source

Long-Term Follow-Up of Health-Related Quality of Life and Short-Term Intervention with CFTR Modulator Therapy in Adults with Cystic Fibrosis: Evaluation of Changes over Several Years with or without 33 Weeks of CFTR Modulator Therapy. [PDF]

Healthcare (Basel), 2023
Gruber W, Welsner M, Blosch C, Dillenhoefer S, Olivier M, Brinkmann F, Koerner-Rettberg C, Sutharsan S, Mellies U, Taube C, Stehling F.   +10 more
europepmc   +1 more source

Novel CFTR Modulators for Treating Cystic Fibrosis [PDF]

ACS Medicinal Chemistry Letters, 2021
openaire   +3 more sources