Beyond the 10%: Unraveling the genetic diversity in Turkish cystic fibrosis patients not eligible for CFTR modulators. [PDF]
Yıldız CA +16 more
europepmc +1 more source
Lentiviral vector gene therapy and CFTR modulators show comparable effectiveness in cystic fibrosis rat airway models. [PDF]
McCarron A +8 more
europepmc +1 more source
Comparison of Reporting Quality in National Cystic Fibrosis Patient Registries: Implications for Identifying Use of Novel CFTR Modulators. [PDF]
Tomlinson OW +2 more
europepmc +1 more source
Allergic bronchopulmonary aspergillosis as an initial manifestation of cystic fibrosis: Diagnostic and therapeutic implications in the era of CFTR modulators. [PDF]
Mitropoulou G +6 more
europepmc +1 more source
Association between CFTR modulators and changes in iron deficiency markers in cystic fibrosis. [PDF]
Jia S +14 more
europepmc +1 more source
Comparison of the Effect of CFTR Modulators <i>elexacaftor</i>/<i>tezacaftor</i>/<i>ivacaftor</i> and <i>lumacaftor</i>/<i>ivacaftor</i> via Serum Human Epididymis Protein 4 Concentration in <i>p.Phe508del-CFTR</i> Homozygous Cystic Fibrosis Patients. [PDF]
Pócsi M +13 more
europepmc +1 more source
Organoid-guided synergistic treatment of minimal function CFTR mutations with CFTR modulators, roflumilast and simvastatin: a personalised approach. [PDF]
Spelier S +6 more
europepmc +1 more source
The Italian external quality assessment program for Cystic Fibrosis sweat chloride test: CFTR modulators and the impact of a new sweat test report form. [PDF]
Cirilli N +10 more
europepmc +1 more source
Erratum: Inflammatory Activity of Epithelial Stem Cell Variants from Cystic Fibrosis Lungs Is Not Resolved by CFTR Modulators. [PDF]
europepmc +1 more source

