Results 251 to 260 of about 55,609,055 (315)

Editorial: Immune-gut-brain axis - a key player in overall human pathologies. [PDF]

open access: yesFront Immunol
Esteves AR   +3 more
europepmc   +1 more source

Plasma EV Proteomics Identifies ECM Remodeling and Inflammatory Proteins LUM and C7 as Candidate Biomarkers in FSHD

open access: yesAnnals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Facioscapulohumeral muscular dystrophy (FSHD) is one of the most debilitating and common muscular dystrophies. Despite its severity, no approved therapy exists for FSHD patients. However, several therapeutic candidates are currently under development, and some have recently entered clinical trials, marking the need for reliable ...
Mustafa Bilal Bayazit   +11 more
wiley   +1 more source

Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan

open access: yesAnnals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito   +8 more
wiley   +1 more source

Patient-reported outcomes in clinical trials leading to breast cancer drug approvals: are we making them count? [PDF]

open access: yesBreast Cancer Res Treat
Margolis S   +7 more
europepmc   +1 more source

Editorial: Abnormal visual processing. [PDF]

open access: yesFront Neurosci
Liu L, Reynaud A, Zhou J.
europepmc   +1 more source

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