Results 251 to 260 of about 1,168,560 (301)

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24‐Month Follow‐Up From the Italian Registry

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane, Giorgia Coratti, Chiara Cutrì, Antonio Varone, Riccardo Masson, Adele D'Amico, Valeria Sansone, Sonia Messina, Federica Ricci, Chiara Ticci, Claudio Bruno, Caterina Agosto, Francesca Benedetti, Antonella Pini, Sabrina Siliquini, Massimiliano Filosto, Alberto Zambon, Ilaria Bitetti, Maria Rosaria Manna, Claudia Dosi, Riccardo Zanin, Stefano Parravicini, Roberto De Sanctis, Giulia Stanca, Michela Catteruccia, Michele Tosi, Irene Mizzoni, Emilio Albamonte, Valentina Franchino, Maria Sframeli, Ilaria Cavallina, Elena Procopio, Michele Sacchini, Simone Morando, Noemi Brolatti, Federica Trucco, Gaia Scarpini, Elena Briganti, Beatrice Berti, Concetta Palermo, Daniela Leone, Stefano C. Previtali, Eugenio Mercuri, the ITASMAC working group   +43 more
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A review of comprehensive utilization of red mud

Waste Management and Research, 2022
Red mud (RM) is a solid waste generated during the process of alumina production. RM has already posed a serious environmental threat with the development of the alumina refining industry. The comprehensive utilization of RM has attracted much attention due to its large-scale generation and harmful nature. This paper introduces the characteristics and
Hongcheng MI
exaly   +3 more sources

Testing subject comprehension of utility questionnaires

Quality of Life Research, 2004
Utility questionnaires are often considered difficult for subjects to understand. Our study reports pilot testing of two subject comprehension tests to determine whether comprehension can be directly measured. Current health utilities were assessed using the standard gamble (SG), time trade-off (TTO), and visual analog scale.
Deborah G, Dobrez, Elizabeth A, Calhoun
openaire   +2 more sources

Utility of comprehensive toxicologic screens in children

The American Journal of Emergency Medicine, 1999
This study was undertaken to evaluate the clinical utility and cost-effectiveness of the limited component versus the high performance liquid chromatography (HPLC) component of comprehensive toxicologic screens in children. A retrospective patient series was studied at the emergency department (ED) of Hughes Spalding Children's Hospital, an urban ...
M G, Belson, H K, Simon
openaire   +2 more sources

The Research on Comprehensive Utilization of Phosphogypsum

Advanced Materials Research, 2013
Introduce several examples of surface active agents used in wet-process phosphoric acid (WPPA) to show its effect on the quality of phosphogypsum. Summarized both domestic and foreign methods of comprehensive utilization of phosphogypsum, such as being made into calcium sulfate whisker, building materials, soil improvement agent, chemical raw materials
Bing Xin Du, Kun Huang
openaire   +1 more source

The utility value of a broad, comprehensive theory of motivation.

Motivation Science, 2023
We provide a brief commentary on the scope and impact of situated expectancy-value theory, as articulated by Eccles and Wigfield in many influential papers. In particular, we consider the long history and legacy of this theory as discussed in their legacy paper (Eccles & Wigfield, 2022).
Judith M. Harackiewicz, Michael W. Asher
openaire   +2 more sources

Comprehensive performance audit of a utility

IEEE Transactions on Energy Conversion, 1991
As part of its efforts to ensure that the utilities are taking all reasonable measures to maintain optimum performance of their power plants, the New York State Department of Public Service (DPS) initiated power-plant performance audits of the seven utilities in the state.
J.R. Wilkinson, P.A. Cropper, D. Blankenhorn, K. Balasubramanian   +3 more
openaire   +1 more source

A new method of comprehensive utilization of rice husk

Journal of Hazardous Materials, 2011
Rice husk is an abundant agricultural byproduct. The research on comprehensive utilization of rice husk to prepare xylose, activated carbon and silica was carried out. The hydrolysis conditions of xylan in rice husk to produce xylose were as follows: the concentration of H(2)SO(4) was 3.6% (wt.%), the temperature was 100°C, the ratio of rice husk mass (
Zichen Wang
exaly   +3 more sources

Comprehensive Utilization of Fly Ash

Advanced Materials Research, 2012
This article has discussed the application of fly ash in the building materials, engineering, farm and industry aspects in detail. At last, it has analyzed the future of application.
Wei Yan, You Li Feng, Ming Gao Yu, Yu Hong Chao   +3 more
openaire   +1 more source

Comprehensive Review on the Utilization of PALF

Advanced Materials Research, 2013
The establishment of high-performance materials made from natural resources is increasing worldwide. Recently, there are exceptional accomplishments in green technology in materials science field via the development on natural fibers utilization due to sustainability and environment issues.
Siti Asia Binti Yahya, Yusri Yusof
openaire   +1 more source