Results 111 to 120 of about 21,009 (196)

Preclinical evaluation of INS1201 AAV9-micro-dystrophin via CSF administration as a potential therapy for Duchenne muscular dystrophy. [PDF]

Mol Ther Adv
Thomsen G, Kaspar A, Ferraiuolo L, Chu B, Garcia VJ, Weiss R, Slaiwa T, Casanova-Vallve N, Cano R, Hurley E, Julazadeh H, Bautista H, Renteria A, Lee M, Rollins J, McAlonis-Downes M, Arnold WD, TreDenick T, Hsu R, Bayless LE, Kozial C, Forespring C, Molony M, Fraser M, Zhou J, Yao J, Bremner SN, Ward SR, Schenk S, Yoshikawa T, Moriyama A, Tsusaki H, Varma S, Kruger M, Stahl M, Kaspar B.   +35 more
europepmc   +1 more source

X-Linked Muscular Dystrophy in a Cat with a Putative Variant in the <i>DMD</i> Gene. [PDF]

Animals (Basel)
Cridge H, Erger C, Thelen Strong K, Guo LT, An H, Xu C, Shelton GD.   +6 more
europepmc   +1 more source

AAV-mediated gene transfer of a novel microdystrophin ameliorates pathology and enhances muscle function in a mouse model of DMD. [PDF]

Mol Ther Nucleic Acids
Owusu L, Kim S, Patel H, Foltz S, Chan GNY, Kim KH, Kopen A, Yang L, Lawlor MW, Buss N, Cunningham JJ, Liu Y, Danos O, Fiscella M.   +13 more
europepmc   +1 more source

Dystrophin in the Nervous System

Brain Pathology, 1996
openaire   +2 more sources

Functional and structural pathologies in skeletal muscle of a rat model of Duchenne muscular dystrophy. [PDF]

Skelet Muscle
Lee YI, Hart CC, Henley-Beasley CS, Herr JS, Zerpa E, Barton ER, Hammers DW, Sweeney HL.   +7 more
europepmc   +1 more source

Dystrophin and Its Isoforms

Brain Pathology, 1996
H M, Sadoulet-Puccio, L M, Kunkel
openaire   +2 more sources

Dystrophin-gene mutation location influences severity of electroretinogram defects in mouse models of Duchenne muscular dystrophy. [PDF]

BMC Med
Liber AMP, Barboni M, Aoki Y, Kremers J, Vaillend C.   +4 more
europepmc   +1 more source

Current Trends in Duchenne Muscular Dystrophy Research and Therapy: 3D Cardiac Modelling. [PDF]

J Cachexia Sarcopenia Muscle
Przymuszała M, Białobrzeska M, Dulak J, Florczyk-Soluch U.   +3 more
europepmc   +1 more source

Multiple modes of AFM reveal distinct mechanical properties for dystrophin and utrophin not manifest by small fragments. [PDF]

Proc Natl Acad Sci U S A
Hua C, Vavra J, Powers J, Muretta JM, Ervasti JM, Salapaka MV.   +5 more
europepmc   +1 more source