Results 221 to 230 of about 127,159 (238)

Targeted Exon Skipping in Transgenic hDMD Mice: A Model for Direct Preclinical Screening of Human-Specific Antisense Oligonucleotides

Molecular Therapy, 2004
Johan T Den Dunnen, Annemieke Aartsma-Rus, Rolf H A M Vossen   +2 more
exaly  

In vivo comparison of 2′-O-methyl phosphorothioate and morpholino antisense oligonucleotides for Duchenne muscular dystrophy exon skipping

Journal of Gene Medicine, 2009
Gert-Jan van Ommen, Annemieke Aartsma-Rus, Judith C T van Deutekom   +2 more
exaly  

Exon skipping therapy for dysferlinopathies

2011
LEVY NICOLAS, KRAHN MARTIN, BARTOLI MARC, GARCIA LUIS   +3 more
openaire   +3 more sources

Becker muscular dystrophy patients with deletions around exon 51; a promising outlook for exon skipping therapy in Duchenne patients

Neuromuscular Disorders, 2010
Bert Bakker, Jan J Verschuuren, Annemieke Aartsma-Rus   +2 more
exaly  

EXON SKIPPING OLIGOMERS FOR MUSCULAR DYSTROPHY

2020
SCHNELL FREDERICK JOSEPH, PASSINI MARCO, ESTRELLA NELSA, HANSON GUNNAR, ZHOU MING, BESTWICK RICHARD   +5 more
openaire   +4 more sources

Exon skipping for dysferlinopathies

2012
Aartsma-Rus, A., Verwey, N., Schneiderat, P., Maarel, S.M. van der, Ommen, G.J.B. van, Houweling-Gazzoli, I.   +5 more
openaire   +1 more source

Staurosporine allows dystrophin expression by skipping of nonsense-encoding exon

Brain and Development, 2016
Masafumi Matsuo, Hiroyuki Awano, Tomoko Lee   +2 more
exaly  

Multiple exon skipping compositions for DMD

2010
SAZANI PETER, KOLE RYSZARD
openaire   +14 more sources

DYSTROPHIN EXON SKIPPING OLIGONUCLEOTIDES

2023
FROELICH STEVEN MICHAEL, WOLOSZYNEK JOSH, MAGAT JENNA-MARIE, VAN DEUTEKOM JUDITH CHRISTINA THEODORA, DE VISSER PETER CHRISTIAN, DATSON NICOLE ANN   +5 more
openaire   +1 more source

MEANS AND METHOD FOR INDUCING EXON-SKIPPING

2007
AARTSMA-RUS ANNEMIEKE, VAN DEUTEKOM JUDITH CHRISTINA THEODORA, VAN OMMEN GARRIT-JAN BOUDEWIJN   +2 more
openaire   +5 more sources