Results 301 to 310 of about 51,494 (318)

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

Lancet, The, 2011
Sebahattin Cirak, V Arechavala-Gomeza, Michela Guglieri   +2 more
exaly  

Exon Skipping

2012
openaire   +1 more source

Exon Skipping

2008
openaire   +1 more source

Exon-skipping therapy for Duchenne muscular dystrophy – Authors' reply

Lancet, The, 2012
Sebahattin Cirak, Karen Anthony
exaly  

Posttranslational Regulation of the Exon Skipping Machinery Controls Aberrant Splicing in Leukemia

Cancer Discovery, 2020
Yalu Zhou, Cuijuan Han, Eric Wang
exaly  

Theoretic applicability of antisense-mediated exon skipping for Duchenne muscular dystrophy mutations

Human Mutation, 2009
Annemieke Aartsma-Rus, Johan T Den Dunnen, Jan J G M Verschuuren   +2 more
exaly  

The promise of selective MET inhibitors in non-small cell lung cancer with MET exon 14 skipping

Cancer Treatment Reviews, 2020
Ravi Salgia, Martin Sattler, Christopher Stroh   +2 more
exaly  

Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers

Nature Medicine, 2015
Kariem Ezzat, Arnaud Ferry, Thomas Voit
exaly  

Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy

Molecular Therapy, 2017
Yusuke Echigoya, Kenji Rowel Q Lim, James S Novak   +2 more
exaly  

Targeted Exon Skipping in Transgenic hDMD Mice: A Model for Direct Preclinical Screening of Human-Specific Antisense Oligonucleotides

Molecular Therapy, 2004
Annemieke Aartsma-Rus, Gert-Jan B Van Ommen, Johan T Den Dunnen   +2 more
exaly