Results 311 to 318 of about 51,494 (318)

Genetic basis of variable exon 9 skipping in cystic fibrosis transmembrane conductance regulator mRNA

Nature Genetics, 1993
Bruce C Trapnell, Garry R Cutting
exaly  

Efficacy of Multi-exon Skipping Treatment in Duchenne Muscular Dystrophy Dog Model Neonates

Molecular Therapy, 2019
Shin’ichi Takeda, Yusuke Echigoya, Tetsuya Nagata   +2 more
exaly  

Exon skipping therapy for DMD.

Journal of neuromuscular diseases, 2022
openaire   +1 more source

New exon-skipping strategy rescues dystrophin

Nature Reviews Drug Discovery, 2015
exaly  

Exon Skipping and Inclusion Therapies

2018
openaire   +1 more source

Exon skipping for dysferlinopathies

2012
Aartsma-Rus, A., Verwey, N., Schneiderat, P., Maarel, S.M. van der, Ommen, G.J.B. van, Houweling-Gazzoli, I.   +5 more
openaire   +1 more source

Exon Skipping Therapies for Rare Kidney Diseases

Journal of the American Society of Nephrology
Tomohiko Yamamura, Kandai Nozu
openaire   +2 more sources

Exon Skipping and Inclusion Therapies

openaire   +1 more source