Results 91 to 100 of about 12,566,431 (163)

Evaluation of One-Stage Assays for the Monitoring of Recombinant Human Factor IX Padua Activity After Etranacogene Dezaparvovec Gene Therapy. [PDF]

Haemophilia
Astermark J, Miesbach W, Coppens M, Gielen S, Twisk J, Dolmetsch R, Verweij S, Monahan PE, Ewenstein BM, Nuthalapati S, Galante N, Young G, HOPE‐B study investigators.   +12 more
europepmc   +1 more source

Evidence of clinically significant extravascular stores of factor IX

Journal of Thrombosis and Haemostasis, 2013
D. Feng, K. Stafford, G. Broze, D. Stafford   +3 more
semanticscholar   +1 more source

Cost-Effectiveness of Recombinant Factor IX Fc Prophylaxis and Recombinant Factor IX On-Demand Treatment in Patients with Haemophilia B Without Inhibitors. [PDF]

Adv Ther
Pochopien M, Tytuła A, Toumi M, Falk A, Martone N, Hakimi Z, Eriksson D.   +6 more
europepmc   +1 more source

Worldwide use of factor IX Padua for hemophilia B gene therapy. [PDF]

Mol Ther, 2022
Samelson-Jones BJ.
europepmc   +1 more source

Factor IX assay discrepancies in the setting of liver gene therapy using a hyperfunctional variant factor IX-Padua. [PDF]

J Thromb Haemost, 2021
Robinson MM, George LA, Carr ME, Samelson-Jones BJ, Arruda VR, Murphy JE, Rybin D, Rupon J, High KA, Tiefenbacher S.   +9 more
europepmc   +1 more source

Real-world usage and effectiveness of recombinant factor IX Fc in haemophilia B from the B-SURE study in France. [PDF]

Ther Adv Hematol
Chambost H, Repessé Y, Genre-Volot F, Desprez D, Castet SM, Vanderbecken S, Zidi M, Gandossi C, Nüesch E, Palmborg H, Santagostino E, B-SURE Study Group.   +11 more
europepmc   +1 more source

Recommendations on the potency labelling of factor VIII and factor IX concentrates

Journal of Thrombosis and Haemostasis, 2013
A. Hubbard, J. Dodt, Timothy K. Lee, K. Mertens, R. Seitz, A. Srivastava, M. Weinstein   +6 more
semanticscholar   +1 more source

Factor IX and deep vein thrombosis

Haematologica, 2009
Gordon Lowe
doaj   +1 more source

Significant PK variability of plasma-derived FIX concentrates in chinese children with Haemophilia B: A fixed single-dose study of factor IX-CTBB. [PDF]

Glob Med Genet
Liu G, Ai D, Li G, Zhen Y, Wu X, Yao W, Wei Y, Li Z, Zhou Y, Wu R, Chen Z.   +10 more
europepmc   +1 more source

Factor IX Padua for haemophilia B gene addition: universal adaptation and repeated success. [PDF]

Lancet Haematol, 2022
George LA.
europepmc   +1 more source