Results 121 to 130 of about 1,008,568 (216)

Generation and Treatment of a Novel Severe Model of Visceral Gaucher Disease by Genetic Therapy. [PDF]

Pharmaceutics
Geard AF, Massaro G, Hughes MP, Arbuthnot P, Waddington SN, Rahim AA.   +5 more
europepmc   +1 more source

Topical miRNA Delivery via Elastic Liposomal Formulation: A Promising Genetic Therapy for Cutaneous Lupus Erythematosus (CLE). [PDF]

Int J Mol Sci
Joseph-Mullol B, Royo M, Preat V, Moliné T, Ferrer B, Aparicio G, Cortés-Hernández J, Solé C.   +7 more
europepmc   +1 more source

Timing of device-aided therapy initiation in Parkinson's disease: reference estimates for healthcare planning and biological heterogeneity. [PDF]

Clin Park Relat Disord
Ledingham D, Stewart CB, Sathyanarayana S, Foster V, Iredale R, Galley D, Baker MR, Pavese N.   +7 more
europepmc   +1 more source

Immunoglobulin GM (γ marker) allotypes expressed on IgG1 as potential genetic markers of response to immune checkpoint blockade therapy. [PDF]

J Immunother Cancer
Pandey JP.
europepmc   +1 more source

Precision Medicine in Inherited Retinal Disease: Advances, Challenges, and Future Directions. [PDF]

J Pers Med
Dhivagaran T, Butt FR, Grover K, Devgan K, Sachdeva K, Dhivagaran V, Abid F, Tao BK, Balas M, Dimopoulos I, Bhatti A.   +10 more
europepmc   +1 more source

Recurrent Intrahepatic Hepatolithiasis Associated With Low-Phospholipid-Associated Cholelithiasis Syndrome: An Underdiagnosed Pathology. [PDF]

ACG Case Rep J
Al Zureikat Q, Guarner-Argente C, Kanth P, Almasarweh N, Jha R, Haddad N.   +5 more
europepmc   +1 more source

Gene Therapy Using Recombinant Adeno-Associated Virus for Leber Congenital Amaurosis Induced by RPE65 Mutation. [PDF]

Clin Ophthalmol
Owliaee I, Teimoori A, Shoushtari M, Shojaeian A.   +3 more
europepmc   +1 more source

Gene Therapy for Cystic Fibrosis Utilizing a Replication Deficient Recombinant Adenovirus Vector to Deliver the Human Cystic Fibrosis Transmembrane Conductance Regulator cDNA to the Airways: A Phase I Study [PDF]

, 1994
Genetic Therapy, Inc.
core  

Metachronous B-Cell Acute Lymphoblastic Leukemia After Localized Neuroblastoma Treated Without Cytotoxic Therapy: A Case Report. [PDF]

Case Rep Hematol
Sedghi R, Nazar Zadeh A, Bordbar M, Zekavat OR, Parand S.   +4 more
europepmc   +1 more source

Synthetic biology of oncolytic bacteria: Comparative microbial chassis and precise killing strategies. [PDF]

Toxicol Rep
Hadid MA, Shaikhli NHA, Suhail OK, Hameed ST, Challoob MA.   +4 more
europepmc   +1 more source