Results 291 to 300 of about 7,770,494 (359)

Identification of amino acids essential for angulin‐1/3 binding of the tricellular tight junction binder, angubindin‐1

FEBS Open Bio, EarlyView.
Angubindin‐1 binds angulin‐1/‐3 at tricellular tight junctions, enhancing intestinal macromolecule permeation. Alanine scanning identified six essential residues (L562, L598, E638, V640, Y643, and K644) of angubindin‐1 critical for binding to angulin‐1/‐3 and permeation‐enhancing activity, providing insights for the development of targeted noninvasive ...
Taiki Kuzu, Yumi Iwashita, Keisuke Tachibana, Itsuki Nishino, Yuki Niwa, Atsuko Uyeda, Kazuki Matsuo, Masahiro Nagahama, Masuo Kondoh   +8 more
wiley   +1 more source

Comprehensive Genomic Profiling in Advanced Non-Small Cell Lung Cancer: A Real-World Cohort Study in Finland. [PDF]

Cancer Med
Hormalainen K, Marttila K, Nykter M, Uibu T, Ahvonen J, Fey V, Keinänen M, Bärlund M, Jukkola A.   +8 more
europepmc   +1 more source

Antisense Oligonucleotide Therapy for Amyotrophic Lateral Sclerosis (ALS): An Umbrella Review. [PDF]

Cureus
Jeong E, Li D.
europepmc   +1 more source

Two Cases of Heterozygous Familial Hypercholesterolemia in Children Effectively Managed With Pitavastatin and Ezetimibe Combination Therapy. [PDF]

Clin Case Rep
Nishioka K, Kondo S, Irie K, Kondo T, Iwase T, Tani R, Inoue T, Matsunaga K, Minamino T, Kusaka T.   +9 more
europepmc   +1 more source

Efficacy of Calcineurin Inhibition in Children With Steroid-Resistant Nephrotic Syndrome. [PDF]

Kidney Int Rep
Khalid M, Schwaderer AL.
europepmc   +1 more source

Regarding "Challenges in diagnosing thrombotic thrombocytopenic purpura". [PDF]

Hematol Transfus Cell Ther
Martins de Oliveira Filho C, Carney BJ.
europepmc   +1 more source

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Genetic therapy for congenital myopathies

Current Opinion in Neurology, 2021
Purpose of review There has been an explosion of advancement in the field of genetic therapies. The first gene-based treatments are now in clinical practice, with several additional therapeutic programs in various stages of development.
Nika Maani, Sophie Karolczak, J. Dowling
semanticscholar   +3 more sources

Clinical Trials of Genetic Therapy with Antisense DNA and DNA Vectors

, 2020
A Brief History of Genetic Therapy: Gene Therapy, Antisense Technology, and Genomics, James W. Hawkins Preclinical Development of Oligonucleotide Therapeutics for Cancer: Regulatory Aspects, Chang-Ho Ahn and Joseph J.
E. Wickstrom
semanticscholar   +1 more source

Cellular Genetic Therapy

Transplantation Proceedings, 2005
Cellular genetic therapy is the ultimate frontier for those pathologies that are consequent to a specific nonfunctional cellular type. A viable cure for there kinds of diseases is the replacement of sick cells with healthy ones, which can be obtained from the same patient or a different donor.
Del Vecchio, F, FILARETO, ANTONIO, SPITALIERI, PAOLA, SANGIUOLO, FEDERICA CARLA, NOVELLI, GIUSEPPE   +4 more
openaire   +5 more sources