Defining the Role of Nurses in Gene Therapy for Haemophilia. [PDF]
Mulders G +5 more
europepmc +1 more source
Gene therapy is revolutionizing treatment paradigms for haemoglobinopathies, establishing a translational framework for disorders that impact red blood cell development. In their paper, Joshi et al. describe the preclinical and early clinical landscape of gene therapies for non‐haemoglobinopathy erythroid disorders and highlight common thematic ...
Gaurav Joshi +3 more
wiley +1 more source
Optimizing Emergency Department Care for People With Bleeding Disorders: A Scoping Review of Barriers and Interventions for Improvement. [PDF]
Guo LY +7 more
europepmc +1 more source
An Automated Microfluidic System for Haemostasis Assessment in Cirrhosis With Thrombocytopenia
ABSTRACT Background & Aims Conventional laboratory tests do not capture platelet–vessel wall interactions (primary haemostasis) occurring in vivo, limiting guidance before invasive procedures. This is relevant in patients with thrombocytopenia, hallmark of advanced cirrhosis. Microfluidic assays may overcome these limitations.
Niccolò Bitto +14 more
wiley +1 more source
Normalization of Haemostasis in People with Haemophilia A: Expert Consensus on Unmet Needs and a Framework for Advancing Towards Health Equity. [PDF]
Hermans C +12 more
europepmc +1 more source
Abstract Background Since the COVID‐19 pandemic, demand for blood products has remained high, while donations have declined. Institutional policies guiding the use of these products may affect their availability, utilisation and waste. We surveyed blood banks (BBs) in the United States (U.S.) to assess policies and practices related to cryoprecipitate ...
Chinelo P. Onyenekwu +3 more
wiley +1 more source
Real-World Unmet Treatment Needs for Patients With Haemophilia: Results From the Global Adelphi Disease Specific Programme Database. [PDF]
Yuste VJ +5 more
europepmc +1 more source
Laboratory Challenges in the Era of Novel Haemophilia Therapies. [PDF]
Rühl H, Miesbach W, Müller J.
europepmc +1 more source
Case Report: Successful concomitant surgical interventions for dilated ascending aorta and aortic valve insufficiency in a severe haemophilia A case. [PDF]
Ursu CE +7 more
europepmc +1 more source

