Haemophilia, EarlyView.Abstract Background Following the approval of the first gene therapies for haemophilia, it is essential to develop an optimal infrastructure for the administration of gene therapy. This can be ensured by identifying the criteria for the definition of treatment centres (hub centres) and follow‐up centres (spoke centres), as well as establishing ...
Wolfgang Miesbach +8 more
wiley +1 more source
Cost analysis of extended half-life recombinant factor IX products in the treatment of haemophilia B in Italy: an update. [PDF]
Glob Reg Health Technol Assess, 2022 Aiello A +5 more
europepmc +1 more source
Pharmacokinetic study of a high‐purity factor IX concentrate (Factor IX Grifols®) with a 6‐month follow up in previously treated patients with severe haemophilia B [PDF]
, 2009 José A. Aznar +8 more
openalex +1 more source
The Roles and Clinical Significance of Major Hepatic‐Derived Metabolites in Hepatocellular Carcinoma
Journal of Gastroenterology and Hepatology, EarlyView.ABSTRACT Hepatocellular carcinoma (HCC) is increasingly recognized as a metabolically orchestrated malignancy, in which hepatic‐derived metabolites function not only as byproducts of liver physiology but also as active modulators of tumor biology.
Rui Sun +5 more
wiley +1 more source
Celecoxib does not delay cutaneous wound healing in haemophilia B mice [PDF]
, 2009 Maureane Hoffman +2 more
openalex +1 more source
Spontaneous urinary bladder rupture in a dog with lymphoplasmacytic cystitis
Journal of Small Animal Practice, EarlyView.A 10‐year‐old male mixed‐breed dog presented with vomiting and anuria. The dog was living indoors, and no trauma was reported by the owner. Ultrasonography and a retrograde urethrogram revealed the presence of a urinary bladder leakage. A celiotomy was performed to repair a urinary bladder tear, along with a biopsy of the urinary bladder wall ...
C. Donà +6 more
wiley +1 more source
Iranian Journal of Allergy, Asthma and Immunology, 2006 Many investigations have proved relations between ABO blood groups with some diseases and factor VIII and von willebrand level in plasma. In this study we investigated a relation between ABO blood groups and factor VIII and IX inhibitors in 102 patients ...
Hassan Mansouri Torghabeh +3 more
doaj
Haemophilia B caused by a missense mutation in the prepeptide sequence of factor IX
, 1993 P. M. Green +4 more
openalex +1 more source
Clinical significance of two mutations in the factor IX gene in a family with haemophilia B [PDF]
, 2009 Adrienne Sexton +5 more
openalex +1 more source
Treatment outcomes in persons with severe haemophilia B in the Nordic region: The B‐NORD study [PDF]
, 2021 Kristina Kihlberg +10 more
openalex +1 more source