Results 161 to 170 of about 9,259 (230)

Bone mineral density in Canadian children with severe haemophilia A or B: a cross-sectional study

, 2021
Cecily Bos, Thuan Minh Tieu, John K. Wu, Karen Strike, Anthony K.C. Chan   +4 more
openalex   +1 more source

Cost-Effectiveness of Recombinant Factor IX Fc Prophylaxis and Recombinant Factor IX On-Demand Treatment in Patients with Haemophilia B Without Inhibitors. [PDF]

Adv Ther
Pochopien M, Tytuła A, Toumi M, Falk A, Martone N, Hakimi Z, Eriksson D.   +6 more
europepmc   +1 more source

Inhibitor incidence in an unselected cohort of previously untreated patients with severe haemophilia B: a PedNet study. [PDF]

Haematologica, 2021
Male C, Andersson NG, Rafowicz A, Liesner R, Kurnik K, Fischer K, Platokouki H, Santagostino E, Chambost H, Nolan B, Königs C, Kenet G, Ljung R, Van den Berg M.   +13 more
europepmc   +1 more source

Plasma‐derived factor VIIa and factor X mixture agent (MC710) prophylaxis in haemophilia B patients with inhibitors

, 2022
Michio Sakai, Kagehiro Amano, Motoaki Chin, Hideyuki Takedani, Hiroyuki Ishida, Kazuo Sakashita, Masashi Taki, Masahiro Migita, Hiroyoshi Watanabe, Masataka Ishimura, Keiji Nogami, Sho Harano, Akira Shirahata   +12 more
openalex   +1 more source

Cost-Effectiveness Analysis of Etranacogene Dezaparvovec Versus Extended Half-Life Prophylaxis for Moderate-to-Severe Haemophilia B in Germany. [PDF]

Pharmacoecon Open
Meier N, Fuchs H, Galactionova K, Hermans C, Pletscher M, Schwenkglenks M.   +5 more
europepmc   +1 more source

Real-World Utilisation and Bleed Rates in Patients with Haemophilia B Who Switched to Recombinant Factor IX Fusion Protein (rIX-FP): A Retrospective International Analysis. [PDF]

Adv Ther, 2020
Hermans C, Marino R, Lambert C, Mangles S, Sommerer P, Rives V, Maro G, Malcangi G.   +7 more
europepmc   +1 more source

Promoterless gene targeting without nucleases ameliorates haemophilia B in mice

, 2014
Adi Barzel, Nicole K. Paulk, Yun Shi, Yuanhua Huang, K. Chu, F. Zhang, Paul N. Valdmanis, Laura Spector, Matthew H. Porteus, K M Gaensler, Mark A. Kay   +10 more
openalex   +2 more sources

Simplifying surgery in haemophilia B: Low factor IX consumption and infrequent infusions in surgical procedures with rIX-FP

, 2020
Julie Curtin, Elena Santagostino, Faraizah Abdul Karim, Yanyan Li, Wilfried Seifert, Claude Négrier   +5 more
openalex   +1 more source

Phase 1-2 Clinical Trial of a Recombinant AAV5 Vector Containing the Human FIX Gene in Patients with Severe or Moderately Severe Haemophilia B

, 2014
Wolfgang Miesbach, C Meyer, Bart Nijmeijer, Florence Salmon, Nadina Grosios, Harald Petry, Frank W.G. Leebeek   +6 more
openalex   +1 more source

Correction to: Nonacog Beta Pegol: A Review in Haemophilia B. [PDF]

Drugs, 2018
Syed YY.
europepmc   +1 more source