Association of factor expression levels with annual bleeding rate in people with haemophilia B. [PDF]
Haemophilia, 2023 Burke T +8 more
europepmc +3 more sources
Factor IX Padua for haemophilia B gene addition: universal adaptation and repeated success. [PDF]
Lancet Haematol, 2022 George LA.
europepmc +3 more sources
Vitamin K deficiency bleeding of newborn masquerading haemophilia B. [PDF]
Sudan J Paediatr, 2020 Kumar M, Kumar S, Bajpayi S, Kumari R.
europepmc +3 more sources
Real-world data demonstrate improved bleed control and extended dosing intervals for patients with haemophilia B after switching to recombinant factor IX Fc fusion protein (rFIXFc) for up to 5 years. [PDF]
Haemophilia, 2020 Shapiro A +8 more
europepmc +3 more sources
Impact of Functional Disability on Quality of Life in Patients with Haemophilia: An Observational Study [PDF]
Journal of Clinical and Diagnostic Research, 2021 Introduction: Haemophilia is a disease characterised by multiple episodes of spontaneous as well as traumatic bleeding leading to joint pains, joint damage.
Ashish Kavi +3 more
doaj +1 more source
Sustained high trough factor IX activity levels with continued use of rIX-FP in adult and paediatric patients with haemophilia B. [PDF]
Haemophilia, 2019 Gill JC, Roberts J, Li Y, Castaman G.
europepmc +3 more sources
Updates in clinical trial data of extended half-life recombinant factor IX products for the treatment of haemophilia B. [PDF]
Ther Adv Hematol, 2018 Mahlangu JN.
europepmc +3 more sources
Gene Therapy in Hemophilia: A Transformational Patient Experience
Journal of Patient Experience, 2023 Hemophilia is a bleeding disorder caused by a single absent/defective gene and characterized by a lack of functional clotting factors. People with hemophilia may experience joint damage, pain, and psychological impairments, all of which could contribute ...
Enayet Rasul +7 more
doaj +1 more source
The B-team: Equal but different?
The Journal of Haemophilia Practice, 2021 As a person with haemophilia B, I have known there are differences between haemophilia A and haemophilia B and their respective treatment throughout my life – though I was shocked when I learnt about the impact inhibitors can have when it comes to ...
Pembroke Luke
doaj +1 more source
South African Family Practice, 2022 Background: Haemophilia A and B are X-linked recessive bleeding disorders resulting from a deficiency of factors VIII and IX, respectively. Early diagnosis and a comprehensive approach to management is mandatory.
Lethukuthula Mafisa +2 more
doaj +1 more source