Results 141 to 150 of about 13,040 (222)

Indirect treatment comparison of iptacopan versus pegcetacoplan for patients with paroxysmal nocturnal hemoglobinuria and residual anemia despite C5 inhibitor treatment. [PDF]

open access: yesJ Comp Eff Res
Kulasekararaj A   +9 more
europepmc   +1 more source

Prognostic significance of PNH clones in aplastic anemia treated with immunosuppression or allogeneic HSCT: a 20-year single-center experience. [PDF]

open access: yesBlood Res
Haroon A   +11 more
europepmc   +1 more source

Successful Birth After First-Trimester Ravulizumab Exposure in a Patient With Paroxysmal Nocturnal Hemoglobinuria: A Case Report. [PDF]

open access: yesEJHaem
Morioka T   +12 more
europepmc   +1 more source

Disease burden and treatment patterns of paroxysmal nocturnal hemoglobinuria in Japan: a real-world survey. [PDF]

open access: yesInt J Hematol
Sakurai M   +10 more
europepmc   +1 more source

Clinical Profile, Humanistic and Economic Burden of Paroxysmal Nocturnal Hemoglobinuria in Patients Treated With C5 Inhibitors. [PDF]

open access: yesEJHaem
Gandhi S   +9 more
europepmc   +1 more source

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