Results 151 to 160 of about 22,402 (256)

Population Pharmacokinetic and Pharmacokinetic/Pharmacodynamic Analyses of Pegcetacoplan in Patients with Paroxysmal Nocturnal Hemoglobinuria

open access: yesDrugs in R&D
Background and Objective Paroxysmal nocturnal hemoglobinuria is a rare blood disorder characterized by life-threatening hemolysis and thrombosis. Complement C5 inhibitor therapy improves symptoms and life prognosis; however, it can result in insufficient
Ryan L. Crass   +4 more
doaj   +1 more source

Hemoglobinuria producida por una fístula en la sutura perivalvular post reemplazo con prótesis valvular mitral

open access: yesActa Médica Peruana, 2001
Se presenta el caso de un paciente de sexo masculino, de 65 años de edad, portador de una cardiopatía isquémica y severo prolapso de la válvula mitral, que fue sometido a cirugía de revascularización con un puente aorto coronario utilizando la vena ...
Régulo Agusti   +2 more
doaj  

Deficiencia de proteínas de superficie en el diagnóstico de hemoglobinuria paroxística nocturna [PDF]

open access: yes
Paroxysmal Nocturnal Hemoglobinuria is a disorder that occurs when there is a mutation, in the PIG-A gene, which\u27s responsible for encoding the glycosylphosphatidylinositol anchored protein class A.
Mena-Zapata, Susana
core  

Anemia and Patient-Reported Outcomes in Patients With Paroxysmal Nocturnal Hemoglobinuria: A Real-World Observational Study. [PDF]

open access: yesEJHaem
Oliva EN   +22 more
europepmc   +1 more source

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