Results 161 to 170 of about 49,324 (252)

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B. [PDF]

N Engl J Med
Reiss UM, Davidoff AM, Tuddenham EGD, Chowdary P, McIntosh J, Muczynski V, Journou M, Simini G, Ireland L, Mohamed S, Riddell A, Pie AJ, Hall A, Quaglia A, Mangles S, Mahlangu J, Haley K, Recht M, Shen YM, Halka KG, Fortner G, Morton CL, Gu Z, Hayden RT, Neufeld EJ, Okhomina VI, Kang G, Nathwani AC.   +27 more
europepmc   +1 more source

Biogen Idec enters hemophilia B market [PDF]

, 2014
Asher Mullard
openalex   +1 more source

Gene therapy as an innovative approach to the treatment of hemophilia B-a review. [PDF]

J Appl Genet
Wróblewska K, Bieszczad D, Popławska M, Ziętara KJ, Zajączkowska M, Filip A.   +5 more
europepmc   +1 more source

A Multicenter Clinical Study of Monoclonal Antibody-Purified Coagulation Factor IX Concentrate (GA-1013) in Treatment of Hemophilia B

, 1991
Hiromu Fukui, Yutaka Yoshida, Yasuyuki Endo, Kazuo Mori, Norio Kobayashi, Juzo Matsuda, M Fujimaki, Minoru Inagaki, Kaneo Yamada, Kojiro Honda, Akira Shibata, Hoyu Takahashi, N Sakuragawa, T Kainuma, Joichi NOMURA, Noriyuki KAWASAKI, J Mimaya, Akira Yoshioka, Shigeru Shirakawa, Katsumi Deguchi, Keiichiro Yoshioka, Hisao Ikari, Eizo Kakishita, Noboru Takata, Akira Shirahata, Kunio Kishida   +25 more
openalex   +2 more sources

Chinese guidance for the clinical application of adeno-associated virus vector-based gene therapy for hemophilia B (2025). [PDF]

Blood Sci
Xue F, Hu Y, Yang R, Sun J, Yang L, Wang X, Yu Z, Zhu T, Zhou H, Zhou Z, Yan Z, Du X, Zheng C, Liu W, Zhou R, Dai J, Yin J, Wang H, Tang LV, Chen S, Cheng H, Zhu M, Wang S, Song Y, Zhang P, Zhang L.   +25 more
europepmc   +1 more source

Gene therapy in an era of emerging treatment options for hemophilia B

, 2015
Paul E. Monahan
openalex   +2 more sources

Hemophilia B With Intracranial Hemorrhage Rehabilitation in High-Dependency Unit: A Case Report. [PDF]

Clin Case Rep
Feng X, Zhu H, Han L, Xu H, He L.
europepmc   +1 more source

The Maintenance of Tolerance After Successful Immune Tolerance Induction in Hemophilia A and B: The North American Registry

, 2000
D. DiMichele, Barbara L. Kroner, Aledort, D. I. Michele, Hulman, Mariani, Lenk, Ciavarella, Berntorp, Scandella   +9 more
openalex   +1 more source

PND33 UTILIZING A PAPER STANDARD GAMBLE INSTRUMENT TO ASSESS HEALTH UTILITY IN PATIENTS WITH HEMOPHILIA B [PDF]

, 2011
Mary Lou, Z.Y. Zhou, Femida Gwadry‐Sridhar, Jiat Ling Poon, Jason N. Doctor, Marion A. Koerper, Megan M. Ullman, K. M. JOHNSON   +7 more
openalex   +1 more source

Somatic mosaicism and female-to-female transmission in a kindred with hemophilia B (factor IX deficiency).

, 1991
Scott A. Taylor, Ken V. Deugau, D Lillicrap   +2 more
openalex   +2 more sources