Results 211 to 220 of about 49,324 (252)

Gene therapy for hemophilia b using pinctm formulated plasmid delivered to muscle with electroporation

, 2000
L. C. Smith, Jason G. Fewell, F.M. MacLaughlin, Vidya Mehta, M. Gondo, François Nicol, Edward M. Nolan, Marjorie S. Read, Timothy C. Nichols, Jeffrey L. Nordstrom   +9 more
openalex   +1 more source

A Case of Epidural Hematoma after Lumbar Spine Surgery in a Hemophilia B Carrier. [PDF]

JMA J
Sakamoto Y, Ozaki T, Tahata S, Fujimoto T, Naruo S.   +4 more
europepmc   +1 more source

Multimodal mechanisms of pathogenic variants in the signal peptide of FIX leading to hemophilia B. [PDF]

Blood Adv
Gao M, Chen L, Yang J, Dong S, Cao Q, Cui Z, Dong Y, Liu H, Shen Y, Yang H, Hao Z, Zhang L, Li W, Tie JK, Shen G.   +14 more
europepmc   +1 more source

The genetic analysis of eight families with hemophilia B in Mongolia: Identification of two novel mutation. [PDF]

Mol Genet Genomic Med
Munkhuu P, Bazarragchaa M, Ichinkhorloo P, Yoo KY, Ayush EA, Batjargal O, Namjil E, Jav S, Purevdorj E, Lkhagvasuren S.   +9 more
europepmc   +1 more source

Clinical data on treatment regimen and use of medication among patients with hemophilia B in Korea. [PDF]

Blood Res
Park YS, Park JK, Park JA, Baek HJ, Lee JH, You CW, Lyu CJ, Choi EJ.   +7 more
europepmc   +1 more source

Hemophilia B and gene therapy: a new chapter with etranacogene dezaparvovec. [PDF]

Blood Adv
Anguela XM, High KA.
europepmc   +1 more source

A transposable element prevents severe hemophilia B and provides insights into the evolution of new- and old world primates. [PDF]

PLoS One
Kopp J, Rovai A, Ott M, Wedemeyer H, Tiede A, Böhmer HJ, Marques T, Langemeier J, Bohne J, Krooss SA.   +9 more
europepmc   +1 more source

Blood coagulation factor IX: structural insights impacting hemophilia B therapy.

Blood
Bos MHA, van Diest RE, Monroe DM.
europepmc   +1 more source

Pharmacokinetic model-based assessment of factor IX prophylaxis treatment regimens in severe hemophilia B. [PDF]

Sci Rep
Vandewalle B, Castaman G, Álvarez-Román MT, Ettingshausen CE, Nemes L, Tomic R, Martins P, Rodrigues JF, Pinachyan K.   +8 more
europepmc   +1 more source