Results 161 to 170 of about 12,467 (245)

Integrating Novel Outcome Measures for Long-Term Evaluation of Lumacaftor-Ivacaftor Therapy in Cystic Fibrosis Patients Homozygous for F508del

Isabella Comello, Francesca Lucca, Silvia Bertolo, Luigi Martinelli, Marco Cipolli, Mirco Ros   +5 more
openalex   +1 more source

Real‐World Improvements of Lung Clearance Index and Ventilation Distribution Efficiency in Children With Cystic Fibrosis After Elexacaftor/Tezacaftor/Ivacaftor Initiation [PDF]

Esben Herborg Henriksen, Rikke Mulvad Sandvik, Mette Frahm Olsen, Tacjana Pressler, Thomas Bryrup, Christian Leo‐Hansen, Bibi Uhre Nielsen, Christine Højte, Marianne Skov, Frederik Buchvald, Inger Hee Mabuza Mathiesen, Tavs Qvist, Hanne Vebert Olesen, Sune Rubak, Camilla Bjørn Jensen, Daniel Faurholt‐Jepsen, Kim G. Nielsen, TransformCF Study Group   +17 more
openalex   +1 more source

Beyond F508del: equity as the next frontier in cystic fibrosis. [PDF]

Lancet Reg Health Am
Cohen RWF, Costa PFBM, Marins KAC, Taulois MM, Barboza ND, Chaves C, Vasconcelos Z, Folescu TW.   +7 more
europepmc   +1 more source

ABCB4 disease-causing variants S242R, S346I, T437I and T1077M significantly impair its function and display differential sensitivity to potentiators. [PDF]

Sci Rep
Madry C, Elbahnsi A, Delaunay JL, Stary A, Lagaye S, Couvert P, Corpechot C, Lemoinne S, Chignard N, Boucherle B, Gautheron J, Décout JL, Callebaut I, Aït-Slimane T.   +13 more
europepmc   +1 more source

Impact of Cystic Fibrosis Transmembrane Conductance Regulator Modulating Therapies on Liver Transplant Outcomes. [PDF]

Gastro Hep Adv
Naimimohasses S, Ray A, Tan E, Wiggins A, Hasjim BJ, Chen S, Bhat M.   +6 more
europepmc   +1 more source

Aging Gracefully: Does Elexacaftor/Tezacaftor/Ivacaftor Safety and Efficacy Stand the Test of Time? [PDF]

Am J Respir Crit Care Med
Wilson G, Hughes D.
europepmc   +1 more source

Hitting the Sweet Spot: The Impact of Elexacaftor/Tezacaftor/Ivacaftor on Glucose Tolerance in Cystic Fibrosis. [PDF]

Am J Respir Crit Care Med
Douglas TA, McMahon SK, Wainwright CE.
europepmc   +1 more source

Fibrose quística: etiopatogénese e novas estratégias terapêuticas [PDF]

, 2013
Ariana Helena Ribeiro de Barros
core  

Lung transplant referral for individuals with cystic fibrosis: Cystic Fibrosis Foundation consensus guidelines [PDF]

, 2019
CF Lung Transplant Referral Guidelines Committee,, Dunitz, Jordan M, Faro, Albert, Gray, Alice L, Hempstead, Sarah E, Lucy, Amy, McKone, Edward F, Pilewski, Joseph M, Ramos, Kathleen J, Rosenbluth, Daniel B, Smith, Patrick J, Tallarico, Erin   +11 more
core   +1 more source

CFTR rescue in W1282X cystic fibrosis patient-derived intestinal organoids (PDIOs) mediated by translational readthrough-inducing drugs (TRIDs). [PDF]

Genet Med Open
Perriera R, Ramalho AS, Vermeulen F, Vitale E, Pibiri I, Pace A, Lentini L.   +6 more
europepmc   +1 more source