Results 91 to 100 of about 2,056 (145)

Mild RPE65-Associated Inherited Retinal Dystrophies: A Multimodal Clinical and Genetic Evaluation. [PDF]

Transl Vis Sci Technol
Wolfram L, Merle DA, Kühlewein L, Kempf M, Stingl K, Kohl S, Stingl K.   +6 more
europepmc   +1 more source

Retinal Viral Gene Therapy: Impact of Route of Administration on Serious Adverse Events-A Systematic Review. [PDF]

Clin Exp Ophthalmol
Berger A, Johnson CD, Marmorstein AD, Scruggs BA.   +3 more
europepmc   +1 more source

Combining modeling approaches for rapid preclinical evaluation of retinal gene therapy. [PDF]

Mol Ther Adv
Saha K.
europepmc   +1 more source

Exosome-based therapeutics: emerging extracellular vesicle platforms for targeted delivery in inherited retinal dystrophies and beyond. [PDF]

Ann Med Surg (Lond)
Khan SA, Ali T, Hameed A, Tahir A, Qamar MA.   +4 more
europepmc   +1 more source

Can Gene Therapy Transform the Treatment Landscape of Posterior Segment Eye Diseases? A Comprehensive Review of Recent Advancements. [PDF]

Drugs
Chen KY, Chan HC, Chan CM.
europepmc   +1 more source

Genetic Therapies for Retinitis Pigmentosa: Current Breakthroughs and Future Directions. [PDF]

J Clin Med
Pniakowska Z, Dzieża N, Kustosik N, Przybylak A, Jurowski P.   +4 more
europepmc   +1 more source

Clinical endpoints special session, ISCEV 2025, Utrecht. [PDF]

Doc Ophthalmol
Hamilton R, Birch D, Stingl K, Fujinami K, Holopigian K, Boon CJF, Moseley J, McAnany JJ, Cideciyan AV, van Genderen MM.   +9 more
europepmc   +1 more source

Advances in Precision Therapeutics and Gene Therapy Applications for Retinal Diseases: Impact and Future Directions. [PDF]

Genes (Basel)
AlEissa MM, Alhawsawi AA, Alonazi R, Magharbil E, Aljahdali A, AlBalawi HB, Alali NM, Hameed S, Abu-Amero KK, Magliyah MS.   +9 more
europepmc   +1 more source

Gene augmentation therapy successfully treats mice with complete congenital stationary night blindness (cCSNB), improving retinal function and visual acuity. [PDF]

Gene Ther
Hasan N, Attaway CA, Di Paolo M, McCall MA, Gregg RG.   +4 more
europepmc   +1 more source

Beyond Numbers: Uses and Value of In-Trial Interview Data for Regulatory and Health Technology Assessment (HTA) Decision Making. [PDF]

Patient
Dias-Barbosa C, Kimel M, Rolska-Wojcik P, Bailey K, Eseyin OR, Martin ML.   +5 more
europepmc   +1 more source