Results 101 to 110 of about 2,056 (145)

Editorial: Retinitis pigmentosa, macular degeneration and related diseases. [PDF]

Front Cell Neurosci
Weiss ER, Han Z.
europepmc   +1 more source

Nanocarrier-Based Gene Delivery Systems: Mechanisms, Clinical Translation, and Future Perspectives. [PDF]

Biotechnol Bioeng
Naqvi RF, Ali M, Zuberi SA, Aamir N, Rafique S.   +4 more
europepmc   +1 more source

Storage and Stability of AAV-Containing Fibrin Hydrogels for Retinal Gene Therapy. [PDF]

Gels
Berger A, Knudsen T, Kopp F, Korda D, Lang M, Scruggs BA, Marmorstein AD.   +6 more
europepmc   +1 more source

Base and Prime Editing for Inherited Retinal Diseases: Delivery Platforms, Safety, Efficacy, and Translational Perspectives. [PDF]

Pharmaceutics
Zhang H, Li Y, Li J, Li X, Li T.
europepmc   +1 more source

Precision Is Not Enough: When Tools Outpace Translation in Ocular Gene Therapy. [PDF]

Genes (Basel)
Abdalla Elsayed MEA, MacLaren RE.
europepmc   +1 more source

Genetic Testing in Inherited Retinal Disease: Current Strategies and Future Directions. [PDF]

J Pers Med
Kang S, Lam BL, Lee W, Berrocal AM, Gregori NZ, Mendoza-Santiesteban CE, Sengillo JD.   +6 more
europepmc   +1 more source

State of the Art on Inherited Retinal Dystrophies: Management and Molecular Genetics. [PDF]

J Clin Med
Nebbioso M, Artico M, Gharbiya M, Mannocci A, Limoli PG, Iannetta D, Donato L.   +6 more
europepmc   +1 more source

When Do Annuity-Based Payments Help to Address the Affordability Challenge of Funding Advanced Therapies? Insights from a Budget Impact Simulation. [PDF]

J Mark Access Health Policy
Van Dyck W, Michelsen S, Veredas D, Huys I, Luyten J, Simoens S.   +5 more
europepmc   +1 more source

Retinitis Pigmentosa: From Genetic Insights to Innovative Therapeutic Approaches-A Literature Review. [PDF]

Medicina (Kaunas)
Murati Calderón RA, Emanuelli A, Izquierdo N.   +2 more
europepmc   +1 more source

Gene Therapy in Rare Genetic Disorders: Current Progress and Future Perspectives. [PDF]

Curr Genomics
Khawaja S, Ali RH, Ahmed I, Umair M.
europepmc   +1 more source