Results 141 to 150 of about 28,823 (151)

Gene therapy for lysosomal storage disorders

Expert Opinion on Biological Therapy, 2001
Enrico Novelli
exaly  

The Relative Frequency of Lysosomal Storage Disorders

Journal of Child Neurology, 2014
Srilatha Kadali, Jayanthi Undamatla
exaly  

Current and emerging therapies for the lysosomal storage disorders

Expert Opinion on Emerging Drugs, 2005
Gregory M Pastores
exaly  

Gene therapy approaches for lysosomal storage disorders, a good model for the treatment of mendelian diseases

Acta Paediatrica, International Journal of Paediatrics, 2012
Rosella Tomanin, Alessandra Zanetti, Francesca D’Avanzo   +2 more
exaly  

Lysosomal Storage Disorders

2022
openaire   +1 more source

Lysosomal Storage Disorders

2009
openaire   +2 more sources

Lysosomal Storage Disorders

2007
John A. Barranger, Mario A. Cabrera-Salazar   +1 more
openaire   +2 more sources

Lysosomal storage disorders

2013
openaire   +1 more source

Lysosomal Storage Disorders

2003
Gregory M. Pastores, Edwin H. Kolodny
openaire   +1 more source

Lysosomal Storage Disorders

2012
openaire   +1 more source