Histone deacetylases in Duchenne muscular dystrophy: a role in the mechanism of disease and a target for inhibition. [PDF]
Bertoldi M +9 more
europepmc +1 more source
Short-term daily deflazacort decreases membrane permeability and increases maximum force in <i>mdx</i> mice. [PDF]
Turner KD +7 more
europepmc +1 more source
Dystrophin Restorative and Compensatory Gene Addition Therapies for Duchenne Muscular Dystrophy: Could CRISPRa Provide a Realistic Alternative? [PDF]
Rostamitehrani Z, Javed R, Popplewell L.
europepmc +1 more source
Mineralocorticoid receptor antagonists reduce inflammatory signaling independent of myofiber mineralocorticoid receptor. [PDF]
Lowe J +5 more
europepmc +1 more source
Tauroursodeoxycholic acid-induced increase in ectopic muscle mineralization occurs exclusively in dystrophic muscles and is independent of endoplasmic reticulum stress. [PDF]
Róg J +11 more
europepmc +1 more source
A combinatorial oligonucleotide therapy to improve dystrophin restoration and dystrophin-deficient muscle health. [PDF]
Moon YJ +6 more
europepmc +1 more source
MicroRNA-33 inhibition ameliorates muscular dystrophy by enhancing skeletal muscle regeneration. [PDF]
Sowa N +32 more
europepmc +1 more source

