Prolonged dystrophin expression and functional correction of mdx mouse muscle following gene transfer with a helper-dependent (gutted) adenovirus-encoding murine dystrophin [PDF]
Rénald Gilbert +5 more
openalex +1 more source
Implications for Cardiac Function Following Rescue of the Dystrophic Diaphragm in a Mouse Model of Duchenne Muscular Dystrophy [PDF]
A Asai +37 more
core +1 more source
Maltodextrin-modified lipoplexes for enhanced mucosal penetration and efficient mRNA delivery. [PDF]
Kopilovic B +6 more
europepmc +1 more source
Expression of dystrophin driven by the 1.35-kb MCK promoter ameliorates muscular dystrophy in fast, but not in slow muscles of transgenic mdx mice [PDF]
Patrick Dunant +7 more
openalex +1 more source
Obligatory and accessory respiratory muscle structure, function and control in early and advanced disease in the mdx mouse model of Duchenne muscular dystrophy. [PDF]
Slyne AD +7 more
europepmc +1 more source
Inhibition of mitochondrial fission protein Drp1 ameliorates skeletal myopathy in the D2-mdx model of Duchenne muscular dystrophy. [PDF]
Rosen HG +11 more
europepmc +1 more source
Enhanced therapeutic potential of a microdystrophin with an extended C-terminal domain. [PDF]
Foltz SJ +10 more
europepmc +1 more source
miR-33 inhibition as a novel therapeutic approach for treating muscular dystrophy. [PDF]
Lopez MA, Alexander MS.
europepmc +1 more source

