Monoclonal IgM antibodies mediate potent complement neutralization by targeting cell-derived epitopes on enveloped viruses. [PDF]
Kainulainen MH +8 more
europepmc +1 more source
Inflammatory response in CF airway epithelial cells: a comparative study of modulators and wild-type CFTR rescue. [PDF]
Kouadri A +6 more
europepmc +1 more source
Disease-Modifying, Neuroprotective Effect of N-Acetyl-l-Leucine in Adult and Pediatric Patients With Niemann-Pick Disease Type C. [PDF]
Patterson MC +16 more
europepmc +1 more source
Serum neurofilament light protein as a biomarker in Niemann-Pick disease, type C1. [PDF]
Cawley NX +11 more
europepmc +1 more source
Real-World Effectiveness and Safety of Eliglustat in Adult Patients with Gaucher Disease Type 1: A Multicenter Retrospective Study in China. [PDF]
Zhou Y, Hao Z, Zhuang Q, Han B.
europepmc +1 more source
Drug-induced urinary incontinence in pediatric patients: A disproportionality analysis of the FDA Adverse Event Reporting System. [PDF]
Jin C, Zhang X, Ouyang X, Lou Q.
europepmc +1 more source
Enzyme replacement therapy for the treatment of late onset Pompe disease: A systematic review and network meta-analysis. [PDF]
Corbett M +9 more
europepmc +1 more source
Integrated bioinformatics analysis of molecular signatures and therapeutic targets in early sepsis. [PDF]
Gai X +9 more
europepmc +1 more source
TOPSIS based multi criteria QSPR modeling of antibiotics using graph theoretic indices. [PDF]
Hashem AF +3 more
europepmc +1 more source
Oral miglustat in homozygous F508del CF patients
Leonard, A. +3 more
openaire +1 more source

