Imputing causality and clonal dynamics from single-cell transcriptomics in paroxysmal nocturnal hemoglobinuria. [PDF]
Mizumaki H +13 more
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Efficacy and safety of crovalimab versus eculizumab in complement inhibitor-naïve patients with paroxysmal nocturnal hemoglobinuria: Chinese subgroup analysis of the phase 3 COMMODORE 2 study. [PDF]
Tong H +10 more
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Efficacy and Safety of Treatments for Paroxysmal Nocturnal Hemoglobinuria: A Systematic Literature Review. [PDF]
Gandhi S +6 more
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Ravulizumab in pregnancy: the case for cautious optimism. [PDF]
Shammo JM.
europepmc +1 more source
Systems Pharmacology Approach to Paroxysmal Nocturnal Hemoglobinuria: Quantitative Framework for Biomarker Dynamics across Multi-Mechanistic Therapies. [PDF]
Cruikshank A +4 more
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American Society of Hematology 2026 guidelines for the diagnosis and management of severe and very severe acquired aplastic anemia. [PDF]
Scheinberg P +25 more
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Paroxysmal nocturnal hemoglobinuria with a positive Coombs test presenting as acute kidney injury: a case report. [PDF]
Jiang L, Chen T, Xu L, Shi M, Huang W.
europepmc +1 more source
Unprovoked Venous Thromboembolism in a Patient with a Small PNH Clone: A Therapeutic Dilemma. [PDF]
Balusu K, Malipeddi D, Phatak P.
europepmc +1 more source
PNH extravascular hemolysis: exploring clinical significance. [PDF]
Notaro R, Risitano AM.
europepmc +1 more source
Epidemiology and care management of Paroxysmal Nocturnal Hemoglobinuria (PNH) in a real-world setting in France: Description from the French National Hospitalization Database. [PDF]
Peffault de Latour R +7 more
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