Results 221 to 226 of about 11,333 (226)

Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

New England Journal of Medicine, 2017
Richard Shell, Linda P Lowes, Lindsay N Alfano   +2 more
exaly  

Selective modulation of the androgen receptor AF2 domain rescues degeneration in spinal bulbar muscular atrophy

Nature Medicine, 2018
James Messing, Nam Chul Kim, Heather S Tillman   +2 more
exaly  

Constitutive muscular abnormalities in culture in spinal muscular atrophy

Lancet, The, 1995
exaly  

Diagnosis of spinal muscular atrophy from fetal normoblasts in maternal blood

Lancet, The, 1998
exaly  

[Case of spinal and bulbar muscular atrophy].

Zhongguo zhen jiu = Chinese acupuncture & moxibustion, 2012
openaire   +1 more source

Screening for spinal muscular atrophy in the UK

Lancet, The
exaly