670. Combined Strategy of Minimal Myeloablation and Optimal BMT Regimen To Cure Murine β-Thalassemia [PDF]
Hady Felfly, Marie Trudel
openalex +1 more source
Analysis of clinical parameters of different types of α-thalassemia children in Hainan region, China. [PDF]
Gao G +10 more
europepmc +1 more source
David Weatherall wins the 2010 Lasker~Koshland Special Achievement Award in Medical Research for advances in thalassemia [PDF]
Kathryn Claiborn
openalex +1 more source
ABSTRACT Backgrounds Hydroxyurea (HU) remains underutilized in adults with sickle cell disease (SCD) despite proven benefits. Current HU guidelines primarily target sickle cell anemia (SCA), overlooking other genotypes. Objectives This study examined HU utilization patterns across genotypes among adults considered to have moderate to severe SCD ...
Siang‐Hao Cheng +4 more
wiley +1 more source
Protein Target Highlights in CASP16: Insights From the Structure Providers
ABSTRACT This article presents an in‐depth analysis of selected CASP16 targets, with a focus on their biological and functional significance. The authors highlight the most relevant features of the target proteins and discuss how well these were reproduced in the submitted predictions.
Leila T. Alexander +34 more
wiley +1 more source
Analysis of Hematological Parameters in Relation to Genotypes in 497 Patients with Hemoglobin H Disease. [PDF]
Lan L, Zheng Z, Wu H.
europepmc +1 more source
Lipid Nanoparticles for Delivery of CRISPR Gene Editing Components
The review presents a comprehensive overview of each component of lipid nanoparticles(LNPs)and their effects on editing efficiency. It specifically highlights strategies for achieving non‐liver delivery, aiming for broader applications in gene editing. Furthermore, this review summarizes the applications of LNPs in gene editing and offers insights for ...
Fan Wu +6 more
wiley +1 more source
Identification of maternal <sup>G</sup>γ(<sup>A</sup>γδβ)<sup>0</sup> thalassemia through retrospective reanalysis of prenatal cfDNA sequencing data. [PDF]
Zhu X +9 more
europepmc +1 more source

