Results 271 to 280 of about 182,088 (307)

CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia

New England Journal of Medicine, 2021
David M Altshuler, Maria Domenica Cappellini, Antonis Kattamis   +2 more
exaly  

Safety and efficacy of thalidomide in patients with transfusion-dependent β-thalassemia: a randomized clinical trial

Signal Transduction and Targeted Therapy, 2021
Weida Wang, Guang-Biao Zhou
exaly  

Thalassemia

Hematology/Oncology Clinics of North America, 2018
openaire   +2 more sources

Thalassemia Revisited

Cell, 1982
D J, Weatherall, J B, Clegg
openaire   +2 more sources

Thalassemia trait or thalassemia intermedia

American Journal of Hematology, 2001
openaire   +2 more sources

The Thalassemias

New England Journal of Medicine, 1976
S H, Orkin, D G, Nathan
openaire   +2 more sources

High levels of GDF15 in thalassemia suppress expression of the iron regulatory protein hepcidin

Nature Medicine, 2007
Sung-Ho Goh, Tomas Ganz, Suthat Fucharoen   +2 more
exaly  

Thalassemia-skull

2022
openaire   +1 more source

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Nature Medicine, 2019
Samantha Scaramuzza, Maria Pia Cicalese, Stefania Galimberti   +2 more
exaly  

Paleontologic Thalassemia

Annals of the New York Academy of Sciences, 1964
openaire   +2 more sources