A Registry-Based Perspective of Interventional Clinical Trials for Duchenne Muscular Dystrophy. [PDF]
Chaudhary JH +4 more
europepmc +1 more source
The highest clinical trial failure rate for any disease in modern medicine: How both amyloid- and non-amyloid-targeting therapies failed to alter disease course in Alzheimer's disease. [PDF]
Guth MAS.
europepmc +1 more source
Is it "Time to Eliminate" Time to Elimination of Symptoms as a Primary Trial End Point for Drugs Targeting Respiratory Viruses? [PDF]
Schiffer JT +4 more
europepmc +1 more source
Does randomization matter in rare disease clinical trials. [PDF]
Wied S +3 more
europepmc +1 more source
A Scoping Literature Review of Digital Measures and Patient-Reported Outcomes for Refractory/Unexplained Chronic Cough: Assessment of Clinical Trials and Real-World Clinical Practice. [PDF]
Skinner EP +4 more
europepmc +1 more source
Cefepime and Mortality: A Systematic Review and Bayesian Meta-Analysis.
Sohani ZN +15 more
europepmc +1 more source

