Results 261 to 270 of about 2,466,381 (317)

Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito, Kamal Benguerba, Ken Tsuchida, Kazushige Yazawa, Isao Tsumiyama, Hiromitsu Kayama, Sandra P. Reyna, Farid Khan, Richard S. Finkel   +8 more
wiley   +1 more source

Correction to "Comprehensive Characterization of Bruton's Tyrosine Kinase Inhibitor Specificity, Potency, and Biological Effects: Insights into Covalent and Noncovalent Mechanistic Signatures". [PDF]

ACS Pharmacol Transl Sci
Darragh AC, Hanna AM, Lipner JH, King AJ, Servant NB, Jahic M.   +5 more
europepmc   +1 more source

Subclinical Optic Nerve Involvement in Radiologically Isolated Syndrome: Multimodal Detection and Diagnostic Impact

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objectives We aimed to determine the frequency of subclinical optic nerve (ON) lesions using MRI, optical coherence tomography (OCT), and visual evoked potentials (VEP) in radiologically isolated syndrome (RIS), and to assess their diagnostic and prognostic significance.
Christine Lebrun‐Frenay, Cassandre Landes‐Château, Lydiane Mondot, Mikael Cohen, Margherita Popolo, Jérôme de Seze, Bertrand Bourre, Françoise Durand‐Dubief, Olivier Casez, Orhun H. Kantarci, Aksel Siva, Stephanie Baillif, Darin T. Okuda, Letizia Leocani   +13 more
wiley   +1 more source

Interplay Between Virulence Genes, Antimicrobial Resistance Profiles, and Biofilm Formation in Klebsiella pneumoniae Causing Urinary Tract Infections in North Lebanon. [PDF]

Microbiologyopen
Zaylaa M, Farha R, Taleb J, Saad A, Gharbawy OE, Sarraf R, Kassam I, Hamdach C, Bissar N.   +8 more
europepmc   +1 more source

Resuscitative thoracotomy in traumatic cardiac arrest : Multisociety consensus recommendations for settings with a low prevalence of penetrating injuries. [PDF]

Wien Klin Wochenschr
Dünser MW, Grassmann D, Hamp T, Krammel M, Eller P, Eisenburger P, Erblich R, Hallmann B, Halmich M, Hellwagner K, Herbich K, Herkner H, Knez I, Negrin LL, Rigaud M, Schlieber J, Schnaubelt S, Schreiber W, Stommel AM, Tomaselli F, Trimmel H, Veigl C, Voelckel W, Watzka S, Wiedemann D, Puchwein P.   +25 more
europepmc   +1 more source

A systemic pharmacovigilance assessment of ophthalmic atropine: signal detection and clinical prioritization from the FAERS database. [PDF]

Front Med (Lausanne)
Xu Z, Liang J, Cai W, Luo Y, Liang F, Lin R, Hu C, Su T, Wu Y, He J, Yu J.   +10 more
europepmc   +1 more source

A Practical Identifiability Criterion Leveraging Weak-Form Parameter Estimation. [PDF]

Bull Math Biol
Heitzman-Breen N, Dukic V, Bortz DM.
europepmc   +1 more source

Genetic diversity in RHD and RHCE genes among a selected Kenyan blood donor population. [PDF]

Transfusion
Sowah SA, Perros AJ, Githiomi R, Lopez GH, Obiero C, Perera TN, Roulis E, Flower RL, Hyland CA.   +8 more
europepmc   +1 more source

Direct Evidence for a Carbon-Carbon One-Electron σ-Bond, or a Weak Carbon-Carbon Interaction? [PDF]

ChemistryOpen
Zazza C, Grandinetti F, Sanna N, Borocci S, Rzepa HS.   +4 more
europepmc   +1 more source